Development of CRISPR_SCD001, an Autologous Hematopoietic Stem Cell Gene Therapy for Sickle Cell Disease after CRISPR-Cas9 Mediated Correction.
- DOI
- 10.1016/j.ymthe.2026.09.020
- Published
- 2026 Sep 19
- Container
- Molecular therapy : the journal of the American Society of Gene Therapy
- Publisher
- Not recorded
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2026.09.020,
title = {Development of CRISPR\_SCD001, an Autologous Hematopoietic Stem Cell Gene Therapy for Sickle Cell Disease after CRISPR-Cas9 Mediated Correction.},
author = {DeWitt M and Campo-Fernandez B and Roy S and Kleinhenz ALW and Davila A and Lennon M and Vu JT and Krishnappa N and Said S and Tseng CH and Park SH and Bao G and Magis W and Martin DIK and Boffelli D and Wyman SK and Kohn DB and Walters MC and Romero Z},
year = {2026},
journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
doi = {10.1016/j.ymthe.2026.09.020},
url = {https://doi.org/10.1016/j.ymthe.2026.09.020}
}RIS
TY - JOUR TI - Development of CRISPR_SCD001, an Autologous Hematopoietic Stem Cell Gene Therapy for Sickle Cell Disease after CRISPR-Cas9 Mediated Correction. AU - DeWitt M AU - Campo-Fernandez B AU - Roy S AU - Kleinhenz ALW AU - Davila A AU - Lennon M AU - Vu JT AU - Krishnappa N AU - Said S AU - Tseng CH AU - Park SH AU - Bao G AU - Magis W AU - Martin DIK AU - Boffelli D AU - Wyman SK AU - Kohn DB AU - Walters MC AU - Romero Z PY - 2026 JO - Molecular therapy : the journal of the American Society of Gene Therapy DO - 10.1016/j.ymthe.2026.09.020 UR - https://doi.org/10.1016/j.ymthe.2026.09.020 ER -
APA
M, D., B, C., S, R., ALW, K., A, D., M, L., JT, V., N, K., S, S., CH, T., SH, P., G, B., W, M., DIK, M., D, B., SK, W., DB, K., MC, W., & Z, R. (2026). Development of CRISPR_SCD001, an Autologous Hematopoietic Stem Cell Gene Therapy for Sickle Cell Disease after CRISPR-Cas9 Mediated Correction.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.09.020
Source records
- pubmed · retrieved 2026-09-25T07:01:31.375Z