Pre-clinical validation of AAV-mediated gene therapy for KCNV2 retinopathy improves visual function and expression in mouse and patient models
- DOI
- 10.1016/j.ymthe.2026.09.025
- Published
- 2026-09
- Container
- Molecular Therapy
- Publisher
- Elsevier BV
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2026.09.025,
title = {Pre-clinical validation of AAV-mediated gene therapy for KCNV2 retinopathy improves visual function and expression in mouse and patient models},
author = {Rabab Rashwan and Paula I. Fuller-Carter and Xin Ru Lim and Alicia A. Brunet and Annie L. Miller and Yashvi Bhatt and Rebekah James and Denise Anderson and Valentina Voigt and Joao A. Paulo and Mehdi Mirzaei and Melissa M. Mangala and Emilie O. Wong and Robyn V. Jamieson and Anai Gonzalez-Cordero and David M. Hunt and Livia S. Carvalho},
year = {2026},
journal = {Molecular Therapy},
doi = {10.1016/j.ymthe.2026.09.025},
url = {https://doi.org/10.1016/j.ymthe.2026.09.025}
}RIS
TY - JOUR TI - Pre-clinical validation of AAV-mediated gene therapy for KCNV2 retinopathy improves visual function and expression in mouse and patient models AU - Rabab Rashwan AU - Paula I. Fuller-Carter AU - Xin Ru Lim AU - Alicia A. Brunet AU - Annie L. Miller AU - Yashvi Bhatt AU - Rebekah James AU - Denise Anderson AU - Valentina Voigt AU - Joao A. Paulo AU - Mehdi Mirzaei AU - Melissa M. Mangala AU - Emilie O. Wong AU - Robyn V. Jamieson AU - Anai Gonzalez-Cordero AU - David M. Hunt AU - Livia S. Carvalho PY - 2026 JO - Molecular Therapy DO - 10.1016/j.ymthe.2026.09.025 UR - https://doi.org/10.1016/j.ymthe.2026.09.025 ER -
APA
Rashwan, R., Fuller-Carter, P. I., Lim, X. R., Brunet, A. A., Miller, A. L., Bhatt, Y., James, R., Anderson, D., Voigt, V., Paulo, J. A., Mirzaei, M., Mangala, M. M., Wong, E. O., Jamieson, R. V., Gonzalez-Cordero, A., Hunt, D. M., & Carvalho, L. S. (2026). Pre-clinical validation of AAV-mediated gene therapy for KCNV2 retinopathy improves visual function and expression in mouse and patient models. Molecular Therapy. https://doi.org/10.1016/j.ymthe.2026.09.025
Source records
- crossref · retrieved 2026-09-25T21:44:18.156Z