Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series

Neil A Shneider, Matthew B Harms, Vlad A Korben, Olivia M Rifai, Benjamin N Hoover, Elizabeth A Harrington, Sonya Aziz-Zaman, Jessica Singleton, Arish Jamil, Vikram R Madan, Julia Yasek, Ikjae Lee, Jinsy A Andrews, Richard M Smiley, Mahabub M Alam, Lauren E Black, Minwook Shin, Jonathan K Watts, David Walk, Daniel Newman, Robert M Pascuzzi, Markus Weber, Christoph Neuwirth, Sandrine Da Cruz, Armand Soriano, Roger Lane, Scott Henry, Joel Mathews, Paymaan Jafar-Nejad, Dan Norris, Frank Rigo, Robert H Brown, Stephan Miller, Rebecca Crean, C Frank Bennett

Open source

DOI: 10.1016/s0140-6736(25)00513-6
Published: 2025-06
Container: The Lancet
Publisher: Elsevier BV
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1016/s0140-6736-25-00513-6,
  title = {Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series},
  author = {Neil A Shneider and Matthew B Harms and Vlad A Korben and Olivia M Rifai and Benjamin N Hoover and Elizabeth A Harrington and Sonya Aziz-Zaman and Jessica Singleton and Arish Jamil and Vikram R Madan and Julia Yasek and Ikjae Lee and Jinsy A Andrews and Richard M Smiley and Mahabub M Alam and Lauren E Black and Minwook Shin and Jonathan K Watts and David Walk and Daniel Newman and Robert M Pascuzzi and Markus Weber and Christoph Neuwirth and Sandrine Da Cruz and Armand Soriano and Roger Lane and Scott Henry and Joel Mathews and Paymaan Jafar-Nejad and Dan Norris and Frank Rigo and Robert H Brown and Stephan Miller and Rebecca Crean and C Frank Bennett},
  year = {2025},
  journal = {The Lancet},
  doi = {10.1016/s0140-6736(25)00513-6},
  url = {https://doi.org/10.1016/s0140-6736(25)00513-6}
}

RIS

TY  - JOUR
TI  - Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series
AU  - Neil A Shneider
AU  - Matthew B Harms
AU  - Vlad A Korben
AU  - Olivia M Rifai
AU  - Benjamin N Hoover
AU  - Elizabeth A Harrington
AU  - Sonya Aziz-Zaman
AU  - Jessica Singleton
AU  - Arish Jamil
AU  - Vikram R Madan
AU  - Julia Yasek
AU  - Ikjae Lee
AU  - Jinsy A Andrews
AU  - Richard M Smiley
AU  - Mahabub M Alam
AU  - Lauren E Black
AU  - Minwook Shin
AU  - Jonathan K Watts
AU  - David Walk
AU  - Daniel Newman
AU  - Robert M Pascuzzi
AU  - Markus Weber
AU  - Christoph Neuwirth
AU  - Sandrine Da Cruz
AU  - Armand Soriano
AU  - Roger Lane
AU  - Scott Henry
AU  - Joel Mathews
AU  - Paymaan Jafar-Nejad
AU  - Dan Norris
AU  - Frank Rigo
AU  - Robert H Brown
AU  - Stephan Miller
AU  - Rebecca Crean
AU  - C Frank Bennett
PY  - 2025
JO  - The Lancet
DO  - 10.1016/s0140-6736(25)00513-6
UR  - https://doi.org/10.1016/s0140-6736(25)00513-6
ER  -

APA

Shneider, N. A., Harms, M. B., Korben, V. A., Rifai, O. M., Hoover, B. N., Harrington, E. A., Aziz-Zaman, S., Singleton, J., Jamil, A., Madan, V. R., Yasek, J., Lee, I., Andrews, J. A., Smiley, R. M., Alam, M. M., Black, L. E., Shin, M., Watts, J. K., Walk, D., Newman, D., Pascuzzi, R. M., Weber, M., Neuwirth, C., Cruz, S. D., Soriano, A., Lane, R., Henry, S., Mathews, J., Jafar-Nejad, P., Norris, D., Rigo, F., Brown, R. H., Miller, S., Crean, R., & Bennett, C. F. (2025). Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series. The Lancet. https://doi.org/10.1016/s0140-6736(25)00513-6

Source records

crossref · retrieved 2026-09-26T01:22:08.304Z