Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.

Mercuri E, Vilchez JJ, Boespflug-Tanguy O, Zaidman CM, Mah JK, Goemans N, Müller-Felber W, Niks EH, Schara-Schmidt U, Bertini E, Comi GP, Mathews KD, Servais L, Vandenborne K, Johannsen J, Messina S, Spinty S, McAdam L, Selby K, Byrne B, Laverty CG, Carroll K, Zardi G, Cazzaniga S, Coceani N, Bettica P, McDonald CM, EPIDYS Study Group

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DOI: 10.1016/s1474-4422(24)00036-x
Published: 2024 Apr
Container: The Lancet. Neurology
Publisher: Not recorded
Open access: no

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Cite this work

BibTeX

@article{allodium:10.1016/s1474-4422-24-00036-x,
  title = {Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.},
  author = {Mercuri E and Vilchez JJ and Boespflug-Tanguy O and Zaidman CM and Mah JK and Goemans N and Müller-Felber W and Niks EH and Schara-Schmidt U and Bertini E and Comi GP and Mathews KD and Servais L and Vandenborne K and Johannsen J and Messina S and Spinty S and McAdam L and Selby K and Byrne B and Laverty CG and Carroll K and Zardi G and Cazzaniga S and Coceani N and Bettica P and McDonald CM and EPIDYS Study Group},
  year = {2024},
  journal = {The Lancet. Neurology},
  doi = {10.1016/s1474-4422(24)00036-x},
  url = {https://doi.org/10.1016/s1474-4422(24)00036-x}
}

RIS

TY  - JOUR
TI  - Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.
AU  - Mercuri E
AU  - Vilchez JJ
AU  - Boespflug-Tanguy O
AU  - Zaidman CM
AU  - Mah JK
AU  - Goemans N
AU  - Müller-Felber W
AU  - Niks EH
AU  - Schara-Schmidt U
AU  - Bertini E
AU  - Comi GP
AU  - Mathews KD
AU  - Servais L
AU  - Vandenborne K
AU  - Johannsen J
AU  - Messina S
AU  - Spinty S
AU  - McAdam L
AU  - Selby K
AU  - Byrne B
AU  - Laverty CG
AU  - Carroll K
AU  - Zardi G
AU  - Cazzaniga S
AU  - Coceani N
AU  - Bettica P
AU  - McDonald CM
AU  - EPIDYS Study Group
PY  - 2024
JO  - The Lancet. Neurology
DO  - 10.1016/s1474-4422(24)00036-x
UR  - https://doi.org/10.1016/s1474-4422(24)00036-x
ER  -

APA

E, M., JJ, V., O, B., CM, Z., JK, M., N, G., W, M., EH, N., U, S., E, B., GP, C., KD, M., L, S., K, V., J, J., S, M., S, S., L, M., K, S., B, B., CG, L., K, C., G, Z., S, C., N, C., P, B., CM, M., & Group, E. S. (2024). Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.. The Lancet. Neurology. https://doi.org/10.1016/s1474-4422(24)00036-x

Source records

pubmed · retrieved 2026-09-26T20:52:28.098Z
europe-pmc · retrieved 2026-09-26T20:52:28.191Z