Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial.

Zielen S, Crawford T, Benatti L, Magnani M, Kieslich M, Ryan M, Meyts I, Gulati S, Borgohain R, Yadav R, Pal P, Hegde A, Kumar S, Venkateswar A, Udani V, Vinayan KP, Nissenkorn A, Fazzi E, Leuzzi V, Stray-Pedersen A, Pietrucha B, Pascual SI, Gouider R, Koenig MK, Wu S, Perlman S, Thye D, Janhofer G, Horn B, Whitehouse W, Lederman H.

Open source

DOI: 10.1016/s1474-4422(24)00220-5
Published: 2024-09-01
Container: Lancet Neurol
Publisher: Not recorded
Open access: no

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Cite this work

BibTeX

@article{allodium:10.1016/s1474-4422-24-00220-5,
  title = {Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial.},
  author = {Zielen S and  Crawford T and  Benatti L and  Magnani M and  Kieslich M and  Ryan M and  Meyts I and  Gulati S and  Borgohain R and  Yadav R and  Pal P and  Hegde A and  Kumar S and  Venkateswar A and  Udani V and  Vinayan KP and  Nissenkorn A and  Fazzi E and  Leuzzi V and  Stray-Pedersen A and  Pietrucha B and  Pascual SI and  Gouider R and  Koenig MK and  Wu S and  Perlman S and  Thye D and  Janhofer G and  Horn B and  Whitehouse W and  Lederman H.},
  year = {2024},
  journal = {Lancet Neurol},
  doi = {10.1016/s1474-4422(24)00220-5},
  url = {https://doi.org/10.1016/s1474-4422(24)00220-5}
}

RIS

TY  - JOUR
TI  - Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial.
AU  - Zielen S
AU  -  Crawford T
AU  -  Benatti L
AU  -  Magnani M
AU  -  Kieslich M
AU  -  Ryan M
AU  -  Meyts I
AU  -  Gulati S
AU  -  Borgohain R
AU  -  Yadav R
AU  -  Pal P
AU  -  Hegde A
AU  -  Kumar S
AU  -  Venkateswar A
AU  -  Udani V
AU  -  Vinayan KP
AU  -  Nissenkorn A
AU  -  Fazzi E
AU  -  Leuzzi V
AU  -  Stray-Pedersen A
AU  -  Pietrucha B
AU  -  Pascual SI
AU  -  Gouider R
AU  -  Koenig MK
AU  -  Wu S
AU  -  Perlman S
AU  -  Thye D
AU  -  Janhofer G
AU  -  Horn B
AU  -  Whitehouse W
AU  -  Lederman H.
PY  - 2024
JO  - Lancet Neurol
DO  - 10.1016/s1474-4422(24)00220-5
UR  - https://doi.org/10.1016/s1474-4422(24)00220-5
ER  -

APA

S, Z., T, C., L, B., M, M., M, K., M, R., I, M., S, G., R, B., R, Y., P, P., A, H., S, K., A, V., V, U., KP, V., A, N., E, F., V, L., A, S., B, P., SI, P., R, G., MK, K., S, W., S, P., D, T., G, J., B, H., W, W., & H., L. (2024). Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial.. Lancet Neurol. https://doi.org/10.1016/s1474-4422(24)00220-5

Source records

europe-pmc · retrieved 2026-09-26T20:27:42.099Z