Safety and efficacy of guanabenz in early-childhood onset vanishing white matter: primary analysis of a single-arm, phase 1/2 trial.

van der Knaap MS, Verbeek RJ, van Voorst RJ, Gonzato E, Stellingwerff MD, Voermans MMC, Postema MC, Dekker H, van den Berg E, Steenweg ME, Bet PM, Bartelink IH, Teunissen CE, Abbink TEM, Berkhof J, van Eekelen R, Wolf NI

Open source

DOI
10.1016/s1474-4422(26)00241-3
Published
2026 Sep
Container
The Lancet. Neurology
Publisher
Not recorded
Open access
unknown

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BibTeX

@article{allodium:10.1016/s1474-4422-26-00241-3,
  title = {Safety and efficacy of guanabenz in early-childhood onset vanishing white matter: primary analysis of a single-arm, phase 1/2 trial.},
  author = {van der Knaap MS and Verbeek RJ and van Voorst RJ and Gonzato E and Stellingwerff MD and Voermans MMC and Postema MC and Dekker H and van den Berg E and Steenweg ME and Bet PM and Bartelink IH and Teunissen CE and Abbink TEM and Berkhof J and van Eekelen R and Wolf NI},
  year = {2026},
  journal = {The Lancet. Neurology},
  doi = {10.1016/s1474-4422(26)00241-3},
  url = {https://doi.org/10.1016/s1474-4422(26)00241-3}
}

RIS

TY  - JOUR
TI  - Safety and efficacy of guanabenz in early-childhood onset vanishing white matter: primary analysis of a single-arm, phase 1/2 trial.
AU  - van der Knaap MS
AU  - Verbeek RJ
AU  - van Voorst RJ
AU  - Gonzato E
AU  - Stellingwerff MD
AU  - Voermans MMC
AU  - Postema MC
AU  - Dekker H
AU  - van den Berg E
AU  - Steenweg ME
AU  - Bet PM
AU  - Bartelink IH
AU  - Teunissen CE
AU  - Abbink TEM
AU  - Berkhof J
AU  - van Eekelen R
AU  - Wolf NI
PY  - 2026
JO  - The Lancet. Neurology
DO  - 10.1016/s1474-4422(26)00241-3
UR  - https://doi.org/10.1016/s1474-4422(26)00241-3
ER  - 

APA

MS, V. D. K., RJ, V., RJ, V. V., E, G., MD, S., MMC, V., MC, P., H, D., E, V. D. B., ME, S., PM, B., IH, B., CE, T., TEM, A., J, B., R, V. E., & NI, W. (2026). Safety and efficacy of guanabenz in early-childhood onset vanishing white matter: primary analysis of a single-arm, phase 1/2 trial.. The Lancet. Neurology. https://doi.org/10.1016/s1474-4422(26)00241-3

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