Expanding the genotypic and phenotypic spectrum of PGAP1 deficiency: clinical and functional insights from 15 patients.

Haase F, Ong OTW, Valenzuela I, Bournazos AM, Amasseri Z, Sheth F, Sheth J, Sheth H, Buchert R, Haack TB, Andrieux J, Liehr T, Kuechler A, de Los Reyes Helices D, Merjane J, Cooper ST, Kinoshita T, Murakami Y, Webster R, Gold W, Lisowski L

Open source

DOI
10.1038/s41431-026-02223-6
Published
2026 Sep 17
Container
European journal of human genetics : EJHG
Publisher
Not recorded
Open access
unknown

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BibTeX

@article{allodium:10.1038/s41431-026-02223-6,
  title = {Expanding the genotypic and phenotypic spectrum of PGAP1 deficiency: clinical and functional insights from 15 patients.},
  author = {Haase F and Ong OTW and Valenzuela I and Bournazos AM and Amasseri Z and Sheth F and Sheth J and Sheth H and Buchert R and Haack TB and Andrieux J and Liehr T and Kuechler A and de Los Reyes Helices D and Merjane J and Cooper ST and Kinoshita T and Murakami Y and Webster R and Gold W and Lisowski L},
  year = {2026},
  journal = {European journal of human genetics : EJHG},
  doi = {10.1038/s41431-026-02223-6},
  url = {https://doi.org/10.1038/s41431-026-02223-6}
}

RIS

TY  - JOUR
TI  - Expanding the genotypic and phenotypic spectrum of PGAP1 deficiency: clinical and functional insights from 15 patients.
AU  - Haase F
AU  - Ong OTW
AU  - Valenzuela I
AU  - Bournazos AM
AU  - Amasseri Z
AU  - Sheth F
AU  - Sheth J
AU  - Sheth H
AU  - Buchert R
AU  - Haack TB
AU  - Andrieux J
AU  - Liehr T
AU  - Kuechler A
AU  - de Los Reyes Helices D
AU  - Merjane J
AU  - Cooper ST
AU  - Kinoshita T
AU  - Murakami Y
AU  - Webster R
AU  - Gold W
AU  - Lisowski L
PY  - 2026
JO  - European journal of human genetics : EJHG
DO  - 10.1038/s41431-026-02223-6
UR  - https://doi.org/10.1038/s41431-026-02223-6
ER  - 

APA

F, H., OTW, O., I, V., AM, B., Z, A., F, S., J, S., H, S., R, B., TB, H., J, A., T, L., A, K., D, D. L. R. H., J, M., ST, C., T, K., Y, M., R, W., W, G., & L, L. (2026). Expanding the genotypic and phenotypic spectrum of PGAP1 deficiency: clinical and functional insights from 15 patients.. European journal of human genetics : EJHG. https://doi.org/10.1038/s41431-026-02223-6

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