FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.

Lacher RK, Henson K, Wathen LN, Jones C, Arnold T, Rice MR, Carles HM, White AR, Ramsuchit E, Murrey D, Raig R, Fisher A, Bucher K, Westerkamp GC, Fritz AL, Gollaway BM, Piloto S, Dismuke D, Robinson JE, Williams MT, Vorhees CV, De Silva EK, Tiwari D, Erickson CA, Pedapati EV, Gross C

Open source

DOI
10.1038/s41434-026-00630-4
Published
2026 Sep
Container
Gene therapy
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1038/s41434-026-00630-4,
  title = {FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.},
  author = {Lacher RK and Henson K and Wathen LN and Jones C and Arnold T and Rice MR and Carles HM and White AR and Ramsuchit E and Murrey D and Raig R and Fisher A and Bucher K and Westerkamp GC and Fritz AL and Gollaway BM and Piloto S and Dismuke D and Robinson JE and Williams MT and Vorhees CV and De Silva EK and Tiwari D and Erickson CA and Pedapati EV and Gross C},
  year = {2026},
  journal = {Gene therapy},
  doi = {10.1038/s41434-026-00630-4},
  url = {https://doi.org/10.1038/s41434-026-00630-4}
}

RIS

TY  - JOUR
TI  - FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.
AU  - Lacher RK
AU  - Henson K
AU  - Wathen LN
AU  - Jones C
AU  - Arnold T
AU  - Rice MR
AU  - Carles HM
AU  - White AR
AU  - Ramsuchit E
AU  - Murrey D
AU  - Raig R
AU  - Fisher A
AU  - Bucher K
AU  - Westerkamp GC
AU  - Fritz AL
AU  - Gollaway BM
AU  - Piloto S
AU  - Dismuke D
AU  - Robinson JE
AU  - Williams MT
AU  - Vorhees CV
AU  - De Silva EK
AU  - Tiwari D
AU  - Erickson CA
AU  - Pedapati EV
AU  - Gross C
PY  - 2026
JO  - Gene therapy
DO  - 10.1038/s41434-026-00630-4
UR  - https://doi.org/10.1038/s41434-026-00630-4
ER  - 

APA

RK, L., K, H., LN, W., C, J., T, A., MR, R., HM, C., AR, W., E, R., D, M., R, R., A, F., K, B., GC, W., AL, F., BM, G., S, P., D, D., JE, R., MT, W., CV, V., EK, D. S., D, T., CA, E., EV, P., & C, G. (2026). FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.. Gene therapy. https://doi.org/10.1038/s41434-026-00630-4

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