FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.
- DOI
- 10.1038/s41434-026-00630-4
- Published
- 2026 Sep
- Container
- Gene therapy
- Publisher
- Not recorded
- Open access
- yes
Credibility signals
limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- cautionDOI registered: No matching Crossref record was present in this response.
- cautionDOI resolves: No matching Crossref record was present in this response.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- supportingOpen access status: Normalized open-access status: open.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- cautionMetadata completeness: 5 of 6 scored descriptive metadata groups are present; missing fields increase uncertainty.
Cite this work
BibTeX
@article{allodium:10.1038/s41434-026-00630-4,
title = {FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.},
author = {Lacher RK and Henson K and Wathen LN and Jones C and Arnold T and Rice MR and Carles HM and White AR and Ramsuchit E and Murrey D and Raig R and Fisher A and Bucher K and Westerkamp GC and Fritz AL and Gollaway BM and Piloto S and Dismuke D and Robinson JE and Williams MT and Vorhees CV and De Silva EK and Tiwari D and Erickson CA and Pedapati EV and Gross C},
year = {2026},
journal = {Gene therapy},
doi = {10.1038/s41434-026-00630-4},
url = {https://doi.org/10.1038/s41434-026-00630-4}
}RIS
TY - JOUR TI - FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome. AU - Lacher RK AU - Henson K AU - Wathen LN AU - Jones C AU - Arnold T AU - Rice MR AU - Carles HM AU - White AR AU - Ramsuchit E AU - Murrey D AU - Raig R AU - Fisher A AU - Bucher K AU - Westerkamp GC AU - Fritz AL AU - Gollaway BM AU - Piloto S AU - Dismuke D AU - Robinson JE AU - Williams MT AU - Vorhees CV AU - De Silva EK AU - Tiwari D AU - Erickson CA AU - Pedapati EV AU - Gross C PY - 2026 JO - Gene therapy DO - 10.1038/s41434-026-00630-4 UR - https://doi.org/10.1038/s41434-026-00630-4 ER -
APA
RK, L., K, H., LN, W., C, J., T, A., MR, R., HM, C., AR, W., E, R., D, M., R, R., A, F., K, B., GC, W., AL, F., BM, G., S, P., D, D., JE, R., MT, W., CV, V., EK, D. S., D, T., CA, E., EV, P., & C, G. (2026). FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.. Gene therapy. https://doi.org/10.1038/s41434-026-00630-4
Source records
- pubmed · retrieved 2026-09-26T00:57:26.341Z
- europe-pmc · retrieved 2026-09-26T00:57:26.351Z