Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates

Michela Milani, Cesare Canepari, Tongyao Liu, Mauro Biffi, Fabio Russo, Tiziana Plati, Rosalia Curto, Susannah Patarroyo-White, Douglas Drager, Ilaria Visigalli, Chiara Brombin, Paola Albertini, Antonia Follenzi, Eduard Ayuso, Christian Mueller, Andrea Annoni, Luigi Naldini, Alessio Cantore

Open source

DOI
10.1038/s41467-022-30102-3
Published
2022-05-04
Container
Nature Communications
Publisher
Springer Science and Business Media LLC
Open access
unknown

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BibTeX

@article{allodium:10.1038/s41467-022-30102-3,
  title = {Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates},
  author = {Michela Milani and Cesare Canepari and Tongyao Liu and Mauro Biffi and Fabio Russo and Tiziana Plati and Rosalia Curto and Susannah Patarroyo-White and Douglas Drager and Ilaria Visigalli and Chiara Brombin and Paola Albertini and Antonia Follenzi and Eduard Ayuso and Christian Mueller and Andrea Annoni and Luigi Naldini and Alessio Cantore},
  year = {2022},
  journal = {Nature Communications},
  doi = {10.1038/s41467-022-30102-3},
  url = {https://doi.org/10.1038/s41467-022-30102-3}
}

RIS

TY  - JOUR
TI  - Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates
AU  - Michela Milani
AU  - Cesare Canepari
AU  - Tongyao Liu
AU  - Mauro Biffi
AU  - Fabio Russo
AU  - Tiziana Plati
AU  - Rosalia Curto
AU  - Susannah Patarroyo-White
AU  - Douglas Drager
AU  - Ilaria Visigalli
AU  - Chiara Brombin
AU  - Paola Albertini
AU  - Antonia Follenzi
AU  - Eduard Ayuso
AU  - Christian Mueller
AU  - Andrea Annoni
AU  - Luigi Naldini
AU  - Alessio Cantore
PY  - 2022
JO  - Nature Communications
DO  - 10.1038/s41467-022-30102-3
UR  - https://doi.org/10.1038/s41467-022-30102-3
ER  - 

APA

Milani, M., Canepari, C., Liu, T., Biffi, M., Russo, F., Plati, T., Curto, R., Patarroyo-White, S., Drager, D., Visigalli, I., Brombin, C., Albertini, P., Follenzi, A., Ayuso, E., Mueller, C., Annoni, A., Naldini, L., & Cantore, A. (2022). Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates. Nature Communications. https://doi.org/10.1038/s41467-022-30102-3

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