Oligodendrocyte-targeted adeno-associated virus gene therapy for Canavan disease in children: a phase 1/2 trial.
- DOI
- 10.1038/s41591-025-03919-w
- Published
- 2025 Nov
- Container
- Nature medicine
- Publisher
- Not recorded
- Open access
- unknown
Credibility signals
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Cite this work
BibTeX
@article{allodium:10.1038/s41591-025-03919-w,
title = {Oligodendrocyte-targeted adeno-associated virus gene therapy for Canavan disease in children: a phase 1/2 trial.},
author = {Leone P and Lober RM and Francis J and Flamini O and Cecil KM and Shera D and Janson CG},
year = {2025},
journal = {Nature medicine},
doi = {10.1038/s41591-025-03919-w},
url = {https://doi.org/10.1038/s41591-025-03919-w}
}RIS
TY - JOUR TI - Oligodendrocyte-targeted adeno-associated virus gene therapy for Canavan disease in children: a phase 1/2 trial. AU - Leone P AU - Lober RM AU - Francis J AU - Flamini O AU - Cecil KM AU - Shera D AU - Janson CG PY - 2025 JO - Nature medicine DO - 10.1038/s41591-025-03919-w UR - https://doi.org/10.1038/s41591-025-03919-w ER -
APA
P, L., RM, L., J, F., O, F., KM, C., D, S., & CG, J. (2025). Oligodendrocyte-targeted adeno-associated virus gene therapy for Canavan disease in children: a phase 1/2 trial.. Nature medicine. https://doi.org/10.1038/s41591-025-03919-w
Source records
- pubmed · retrieved 2026-09-27T01:33:03.431Z