Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial.
- DOI
- 10.1038/s41591-025-04103-w
- Published
- 2025-12-08
- Container
- Nat Med
- Publisher
- Not recorded
- Open access
- yes
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Cite this work
BibTeX
@article{allodium:10.1038/s41591-025-04103-w,
title = {Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial.},
author = {Proud CM and Vũ DC and Wilmshurst JM and Sanmaneechai O and Gulati S and Xiong H and Moreno HC and Tay SKH and Thong MK and Born AP and Banzzatto Ortega A and Jong YJ and Al-Muhaizea MA and Lee AW and Visootsak J and Tauscher-Wisniewski S and Alecu I and Parlikar R and Finkel RS and STEER Study Group.},
year = {2026},
journal = {Nat Med},
doi = {10.1038/s41591-025-04103-w},
url = {https://doi.org/10.1038/s41591-025-04103-w}
}RIS
TY - JOUR TI - Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial. AU - Proud CM AU - Vũ DC AU - Wilmshurst JM AU - Sanmaneechai O AU - Gulati S AU - Xiong H AU - Moreno HC AU - Tay SKH AU - Thong MK AU - Born AP AU - Banzzatto Ortega A AU - Jong YJ AU - Al-Muhaizea MA AU - Lee AW AU - Visootsak J AU - Tauscher-Wisniewski S AU - Alecu I AU - Parlikar R AU - Finkel RS AU - STEER Study Group. PY - 2026 JO - Nat Med DO - 10.1038/s41591-025-04103-w UR - https://doi.org/10.1038/s41591-025-04103-w ER -
APA
CM, P., DC, V., JM, W., O, S., S, G., H, X., HC, M., SKH, T., MK, T., AP, B., A, B. O., YJ, J., MA, A., AW, L., J, V., S, T., I, A., R, P., RS, F., & Group., S. S. (2026). Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial.. Nat Med. https://doi.org/10.1038/s41591-025-04103-w
Source records
- europe-pmc · retrieved 2026-11-10T13:37:41.842Z