Factor IX Padua AAV gene therapy in adolescents with hemophilia B: a phase 1 trial.

Xue F, Zhang A, Ju M, Wu X, Xu B, Pei X, Wang Y, Liu W, Liu A, Jiang W, Dai X, Chen Y, Liu X, Fu R, Sun T, Gu W, Zheng J, Du Z, Yang C, Xiao X, Yang R, Hu Q, Zhang L.

Open source

DOI: 10.1038/s41591-026-04636-8
Published: 2026-09-16
Container: Nat Med
Publisher: Not recorded
Open access: no

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Cite this work

BibTeX

@article{allodium:10.1038/s41591-026-04636-8,
  title = {Factor IX Padua AAV gene therapy in adolescents with hemophilia B: a phase 1 trial.},
  author = {Xue F and  Zhang A and  Ju M and  Wu X and  Xu B and  Pei X and  Wang Y and  Liu W and  Liu A and  Jiang W and  Dai X and  Chen Y and  Liu X and  Fu R and  Sun T and  Gu W and  Zheng J and  Du Z and  Yang C and  Xiao X and  Yang R and  Hu Q and  Zhang L.},
  year = {2026},
  journal = {Nat Med},
  doi = {10.1038/s41591-026-04636-8},
  url = {https://doi.org/10.1038/s41591-026-04636-8}
}

RIS

TY  - JOUR
TI  - Factor IX Padua AAV gene therapy in adolescents with hemophilia B: a phase 1 trial.
AU  - Xue F
AU  -  Zhang A
AU  -  Ju M
AU  -  Wu X
AU  -  Xu B
AU  -  Pei X
AU  -  Wang Y
AU  -  Liu W
AU  -  Liu A
AU  -  Jiang W
AU  -  Dai X
AU  -  Chen Y
AU  -  Liu X
AU  -  Fu R
AU  -  Sun T
AU  -  Gu W
AU  -  Zheng J
AU  -  Du Z
AU  -  Yang C
AU  -  Xiao X
AU  -  Yang R
AU  -  Hu Q
AU  -  Zhang L.
PY  - 2026
JO  - Nat Med
DO  - 10.1038/s41591-026-04636-8
UR  - https://doi.org/10.1038/s41591-026-04636-8
ER  -

APA

F, X., A, Z., M, J., X, W., B, X., X, P., Y, W., W, L., A, L., W, J., X, D., Y, C., X, L., R, F., T, S., W, G., J, Z., Z, D., C, Y., X, X., R, Y., Q, H., & L., Z. (2026). Factor IX Padua AAV gene therapy in adolescents with hemophilia B: a phase 1 trial.. Nat Med. https://doi.org/10.1038/s41591-026-04636-8

Source records

europe-pmc · retrieved 2026-09-25T17:29:33.619Z