Mifepristone alone and in combination with scAAV9-SMN1 gene therapy improves disease phenotypes in Smn(2B/-) spinal muscular atrophy mice.

Sutton ER, McCallion E, Hoolachan JM, Çetin Ö, Pacheco-Torres P, Rashid S, Bouhmidi S, Haynes K, Churchill L, Scaife T, Chaytow H, Huang YT, Duguez S, Schneider BL, Gillingwater TH, Dimitriadi M, Bowerman M

Open source

DOI
10.1038/s41598-025-24050-3
Published
2025 Nov 17
Container
Scientific reports
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1038/s41598-025-24050-3,
  title = {Mifepristone alone and in combination with scAAV9-SMN1 gene therapy improves disease phenotypes in Smn(2B/-) spinal muscular atrophy mice.},
  author = {Sutton ER and McCallion E and Hoolachan JM and Çetin Ö and Pacheco-Torres P and Rashid S and Bouhmidi S and Haynes K and Churchill L and Scaife T and Chaytow H and Huang YT and Duguez S and Schneider BL and Gillingwater TH and Dimitriadi M and Bowerman M},
  year = {2025},
  journal = {Scientific reports},
  doi = {10.1038/s41598-025-24050-3},
  url = {https://doi.org/10.1038/s41598-025-24050-3}
}

RIS

TY  - JOUR
TI  - Mifepristone alone and in combination with scAAV9-SMN1 gene therapy improves disease phenotypes in Smn(2B/-) spinal muscular atrophy mice.
AU  - Sutton ER
AU  - McCallion E
AU  - Hoolachan JM
AU  - Çetin Ö
AU  - Pacheco-Torres P
AU  - Rashid S
AU  - Bouhmidi S
AU  - Haynes K
AU  - Churchill L
AU  - Scaife T
AU  - Chaytow H
AU  - Huang YT
AU  - Duguez S
AU  - Schneider BL
AU  - Gillingwater TH
AU  - Dimitriadi M
AU  - Bowerman M
PY  - 2025
JO  - Scientific reports
DO  - 10.1038/s41598-025-24050-3
UR  - https://doi.org/10.1038/s41598-025-24050-3
ER  - 

APA

ER, S., E, M., JM, H., Ö, Ç., P, P., S, R., S, B., K, H., L, C., T, S., H, C., YT, H., S, D., BL, S., TH, G., M, D., & M, B. (2025). Mifepristone alone and in combination with scAAV9-SMN1 gene therapy improves disease phenotypes in Smn(2B/-) spinal muscular atrophy mice.. Scientific reports. https://doi.org/10.1038/s41598-025-24050-3

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