Pre-clinical development of AP4B1 gene replacement therapy for hereditary spastic paraplegia type 47.

Wiseman JP, Scarrott JM, Alves-Cruzeiro J, Saffari A, Böger C, Karyka E, Dawes E, Davies AK, Marchi PM, Graves E, Fernandes F, Yang ZL, Coldicott I, Hirst J, Webster CP, Highley JR, Hackett N, Angyal A, Silva T, Higginbottom A, Shaw PJ, Ferraiuolo L, Ebrahimi-Fakhari D, Azzouz M

Open source

DOI
10.1038/s44321-024-00148-5
Published
2024 Nov
Container
EMBO molecular medicine
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1038/s44321-024-00148-5,
  title = {Pre-clinical development of AP4B1 gene replacement therapy for hereditary spastic paraplegia type 47.},
  author = {Wiseman JP and Scarrott JM and Alves-Cruzeiro J and Saffari A and Böger C and Karyka E and Dawes E and Davies AK and Marchi PM and Graves E and Fernandes F and Yang ZL and Coldicott I and Hirst J and Webster CP and Highley JR and Hackett N and Angyal A and Silva T and Higginbottom A and Shaw PJ and Ferraiuolo L and Ebrahimi-Fakhari D and Azzouz M},
  year = {2024},
  journal = {EMBO molecular medicine},
  doi = {10.1038/s44321-024-00148-5},
  url = {https://doi.org/10.1038/s44321-024-00148-5}
}

RIS

TY  - JOUR
TI  - Pre-clinical development of AP4B1 gene replacement therapy for hereditary spastic paraplegia type 47.
AU  - Wiseman JP
AU  - Scarrott JM
AU  - Alves-Cruzeiro J
AU  - Saffari A
AU  - Böger C
AU  - Karyka E
AU  - Dawes E
AU  - Davies AK
AU  - Marchi PM
AU  - Graves E
AU  - Fernandes F
AU  - Yang ZL
AU  - Coldicott I
AU  - Hirst J
AU  - Webster CP
AU  - Highley JR
AU  - Hackett N
AU  - Angyal A
AU  - Silva T
AU  - Higginbottom A
AU  - Shaw PJ
AU  - Ferraiuolo L
AU  - Ebrahimi-Fakhari D
AU  - Azzouz M
PY  - 2024
JO  - EMBO molecular medicine
DO  - 10.1038/s44321-024-00148-5
UR  - https://doi.org/10.1038/s44321-024-00148-5
ER  - 

APA

JP, W., JM, S., J, A., A, S., C, B., E, K., E, D., AK, D., PM, M., E, G., F, F., ZL, Y., I, C., J, H., CP, W., JR, H., N, H., A, A., T, S., A, H., PJ, S., L, F., D, E., & M, A. (2024). Pre-clinical development of AP4B1 gene replacement therapy for hereditary spastic paraplegia type 47.. EMBO molecular medicine. https://doi.org/10.1038/s44321-024-00148-5

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