A Phase 3 Trial of Vosoritide in Children with Hypochondroplasia.

Dauber A, Savarirayan R, Campeau PM, Carroll RS, Cheung M, Cormier-Daire V, de Bergua JM, Edouard T, Gonfiantini MV, Hoover-Fong J, Kannu P, Kinoshita Y, Kubota T, Mendoza-Londono R, Namba N, Ohata Y, Onesimo R, Palm K, Prada CE, Reynaud R, Rossi M, Semler O, Takasawa K, Bassi R, Ghani S, Huntsman Labed A, Osmond D, Sabir I, White J, Maghnie M

Open source

DOI: 10.1056/evidoa2600257
Published: 2026 Sep 9
Container: NEJM evidence
Publisher: Not recorded
Open access: no

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limited evidence Score 43/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

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Cite this work

BibTeX

@article{allodium:10.1056/evidoa2600257,
  title = {A Phase 3 Trial of Vosoritide in Children with Hypochondroplasia.},
  author = {Dauber A and Savarirayan R and Campeau PM and Carroll RS and Cheung M and Cormier-Daire V and de Bergua JM and Edouard T and Gonfiantini MV and Hoover-Fong J and Kannu P and Kinoshita Y and Kubota T and Mendoza-Londono R and Namba N and Ohata Y and Onesimo R and Palm K and Prada CE and Reynaud R and Rossi M and Semler O and Takasawa K and Bassi R and Ghani S and Huntsman Labed A and Osmond D and Sabir I and White J and Maghnie M},
  year = {2026},
  journal = {NEJM evidence},
  doi = {10.1056/evidoa2600257},
  url = {https://doi.org/10.1056/evidoa2600257}
}

RIS

TY  - JOUR
TI  - A Phase 3 Trial of Vosoritide in Children with Hypochondroplasia.
AU  - Dauber A
AU  - Savarirayan R
AU  - Campeau PM
AU  - Carroll RS
AU  - Cheung M
AU  - Cormier-Daire V
AU  - de Bergua JM
AU  - Edouard T
AU  - Gonfiantini MV
AU  - Hoover-Fong J
AU  - Kannu P
AU  - Kinoshita Y
AU  - Kubota T
AU  - Mendoza-Londono R
AU  - Namba N
AU  - Ohata Y
AU  - Onesimo R
AU  - Palm K
AU  - Prada CE
AU  - Reynaud R
AU  - Rossi M
AU  - Semler O
AU  - Takasawa K
AU  - Bassi R
AU  - Ghani S
AU  - Huntsman Labed A
AU  - Osmond D
AU  - Sabir I
AU  - White J
AU  - Maghnie M
PY  - 2026
JO  - NEJM evidence
DO  - 10.1056/evidoa2600257
UR  - https://doi.org/10.1056/evidoa2600257
ER  -

APA

A, D., R, S., PM, C., RS, C., M, C., V, C., JM, D. B., T, E., MV, G., J, H., P, K., Y, K., T, K., R, M., N, N., Y, O., R, O., K, P., CE, P., R, R., M, R., O, S., K, T., R, B., S, G., A, H. L., D, O., I, S., J, W., & M, M. (2026). A Phase 3 Trial of Vosoritide in Children with Hypochondroplasia.. NEJM evidence. https://doi.org/10.1056/evidoa2600257

Source records

pubmed · retrieved 2026-09-25T18:06:52.088Z
europe-pmc · retrieved 2026-09-25T18:06:52.106Z