In Vivo Base Editing of <i>PCSK9</i> with VERVE-102 for Hypercholesterolemia

Scott B. Vafai, Jörg Täubel, Thomas Ashdown, Riyaz S. Patel, Sadaf Diamondali, Jaimini Cegla, Handrean Soran, Bilal Bashir, Alexander Abitbol, Daniel Gaudet, Alex Lauzière, Liam R. Brunham, David E. Newby, Stephen J. Nicholls, Russell S. Scott, Jane Kerr, Jean-Claude Tardif, Catherine Lunken, Steve E. Humphries, Verena Karsten, Patrick D. Tyler, Xinyan Zhang, Nidal Huniti, Patrick A. Flight, Chelsey L. Jensen, Rick Falzone, Joseph C. Biedenkapp, Troy Lister, Leslie E. Stolz, Amit V. Khera, Sekar Kathiresan

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DOI: 10.1056/nejmoa2601283
Published: 2026-08-13
Container: New England Journal of Medicine
Publisher: Massachusetts Medical Society
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1056/nejmoa2601283,
  title = {In Vivo Base Editing of
                    <i>PCSK9</i>
                    with VERVE-102 for Hypercholesterolemia},
  author = {Scott B. Vafai and Jörg Täubel and Thomas Ashdown and Riyaz S. Patel and Sadaf Diamondali and Jaimini Cegla and Handrean Soran and Bilal Bashir and Alexander Abitbol and Daniel Gaudet and Alex Lauzière and Liam R. Brunham and David E. Newby and Stephen J. Nicholls and Russell S. Scott and Jane Kerr and Jean-Claude Tardif and Catherine Lunken and Steve E. Humphries and Verena Karsten and Patrick D. Tyler and Xinyan Zhang and Nidal Huniti and Patrick A. Flight and Chelsey L. Jensen and Rick Falzone and Joseph C. Biedenkapp and Troy Lister and Leslie E. Stolz and Amit V. Khera and Sekar Kathiresan},
  year = {2026},
  journal = {New England Journal of Medicine},
  doi = {10.1056/nejmoa2601283},
  url = {https://doi.org/10.1056/nejmoa2601283}
}

RIS

TY  - JOUR
TI  - In Vivo Base Editing of
                    <i>PCSK9</i>
                    with VERVE-102 for Hypercholesterolemia
AU  - Scott B. Vafai
AU  - Jörg Täubel
AU  - Thomas Ashdown
AU  - Riyaz S. Patel
AU  - Sadaf Diamondali
AU  - Jaimini Cegla
AU  - Handrean Soran
AU  - Bilal Bashir
AU  - Alexander Abitbol
AU  - Daniel Gaudet
AU  - Alex Lauzière
AU  - Liam R. Brunham
AU  - David E. Newby
AU  - Stephen J. Nicholls
AU  - Russell S. Scott
AU  - Jane Kerr
AU  - Jean-Claude Tardif
AU  - Catherine Lunken
AU  - Steve E. Humphries
AU  - Verena Karsten
AU  - Patrick D. Tyler
AU  - Xinyan Zhang
AU  - Nidal Huniti
AU  - Patrick A. Flight
AU  - Chelsey L. Jensen
AU  - Rick Falzone
AU  - Joseph C. Biedenkapp
AU  - Troy Lister
AU  - Leslie E. Stolz
AU  - Amit V. Khera
AU  - Sekar Kathiresan
PY  - 2026
JO  - New England Journal of Medicine
DO  - 10.1056/nejmoa2601283
UR  - https://doi.org/10.1056/nejmoa2601283
ER  -

APA

Vafai, S. B., Täubel, J., Ashdown, T., Patel, R. S., Diamondali, S., Cegla, J., Soran, H., Bashir, B., Abitbol, A., Gaudet, D., Lauzière, A., Brunham, L. R., Newby, D. E., Nicholls, S. J., Scott, R. S., Kerr, J., Tardif, J., Lunken, C., Humphries, S. E., Karsten, V., Tyler, P. D., Zhang, X., Huniti, N., Flight, P. A., Jensen, C. L., Falzone, R., Biedenkapp, J. C., Lister, T., Stolz, L. E., Khera, A. V., & Kathiresan, S. (2026). In Vivo Base Editing of <i>PCSK9</i> with VERVE-102 for Hypercholesterolemia. New England Journal of Medicine. https://doi.org/10.1056/nejmoa2601283

Source records

crossref · retrieved 2026-09-27T00:31:08.831Z