Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease.

Frangoul H, de la Fuente J, Chopra Y, Meisel R, Amrolia PJ, Algeri M, Sharma A, Cappellini MD, Corbacioglu S, Kattamis A, Lobitz S, de Montalembert M, Rondelli D, Sheth S, Steinberg MH, Walters MC, Boerner K, Liu T, Zairis S, Hobbs W, Grupp SA, Locatelli F, CLIMB THAL-141 and CLIMB SCD-151 Study Groups

Open source

DOI: 10.1056/nejmoa2603387
Published: 2026 Sep 10
Container: The New England journal of medicine
Publisher: Not recorded
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1056/nejmoa2603387,
  title = {Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease.},
  author = {Frangoul H and de la Fuente J and Chopra Y and Meisel R and Amrolia PJ and Algeri M and Sharma A and Cappellini MD and Corbacioglu S and Kattamis A and Lobitz S and de Montalembert M and Rondelli D and Sheth S and Steinberg MH and Walters MC and Boerner K and Liu T and Zairis S and Hobbs W and Grupp SA and Locatelli F and CLIMB THAL-141 and CLIMB SCD-151 Study Groups},
  year = {2026},
  journal = {The New England journal of medicine},
  doi = {10.1056/nejmoa2603387},
  url = {https://doi.org/10.1056/nejmoa2603387}
}

RIS

TY  - JOUR
TI  - Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease.
AU  - Frangoul H
AU  - de la Fuente J
AU  - Chopra Y
AU  - Meisel R
AU  - Amrolia PJ
AU  - Algeri M
AU  - Sharma A
AU  - Cappellini MD
AU  - Corbacioglu S
AU  - Kattamis A
AU  - Lobitz S
AU  - de Montalembert M
AU  - Rondelli D
AU  - Sheth S
AU  - Steinberg MH
AU  - Walters MC
AU  - Boerner K
AU  - Liu T
AU  - Zairis S
AU  - Hobbs W
AU  - Grupp SA
AU  - Locatelli F
AU  - CLIMB THAL-141 and CLIMB SCD-151 Study Groups
PY  - 2026
JO  - The New England journal of medicine
DO  - 10.1056/nejmoa2603387
UR  - https://doi.org/10.1056/nejmoa2603387
ER  -

APA

H, F., J, D. L. F., Y, C., R, M., PJ, A., M, A., A, S., MD, C., S, C., A, K., S, L., M, D. M., D, R., S, S., MH, S., MC, W., K, B., T, L., S, Z., W, H., SA, G., F, L., & Groups, C. T. A. C. S. S. (2026). Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease.. The New England journal of medicine. https://doi.org/10.1056/nejmoa2603387

Source records

pubmed · retrieved 2026-09-26T21:11:42.212Z