Leveraging external control for accelerating development: A case study from cell gene therapy in Duchenne muscular dystrophy.

Li H, Roychoudhury S, Shi H, Gundapaneni B, Gamalo M

DOI: 10.1080/10543406.2026.2729799
Published: 2026 Sep 20
Container: Journal of biopharmaceutical statistics
Publisher: Not recorded
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1080/10543406.2026.2729799,
  title = {Leveraging external control for accelerating development: A case study from cell gene therapy in Duchenne muscular dystrophy.},
  author = {Li H and Roychoudhury S and Shi H and Gundapaneni B and Gamalo M},
  year = {2026},
  journal = {Journal of biopharmaceutical statistics},
  doi = {10.1080/10543406.2026.2729799},
  url = {https://doi.org/10.1080/10543406.2026.2729799}
}

RIS

TY  - JOUR
TI  - Leveraging external control for accelerating development: A case study from cell gene therapy in Duchenne muscular dystrophy.
AU  - Li H
AU  - Roychoudhury S
AU  - Shi H
AU  - Gundapaneni B
AU  - Gamalo M
PY  - 2026
JO  - Journal of biopharmaceutical statistics
DO  - 10.1080/10543406.2026.2729799
UR  - https://doi.org/10.1080/10543406.2026.2729799
ER  -

APA

H, L., S, R., H, S., B, G., & M, G. (2026). Leveraging external control for accelerating development: A case study from cell gene therapy in Duchenne muscular dystrophy.. Journal of biopharmaceutical statistics. https://doi.org/10.1080/10543406.2026.2729799

Source records

pubmed · retrieved 2026-09-26T01:36:16.673Z