Development of Exon Skipping Therapies for Duchenne Muscular Dystrophy: A Critical Review and a Perspective on the Outstanding Issues.

Aartsma-Rus A, Straub V, Hemmings R, Haas M, Schlosser-Weber G, Stoyanova-Beninska V, Mercuri E, Muntoni F, Sepodes B, Vroom E, Balabanov P

Open source

DOI: 10.1089/nat.2017.0682
Published: 2017 Oct
Container: Nucleic acid therapeutics
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1089/nat.2017.0682,
  title = {Development of Exon Skipping Therapies for Duchenne Muscular Dystrophy: A Critical Review and a Perspective on the Outstanding Issues.},
  author = {Aartsma-Rus A and Straub V and Hemmings R and Haas M and Schlosser-Weber G and Stoyanova-Beninska V and Mercuri E and Muntoni F and Sepodes B and Vroom E and Balabanov P},
  year = {2017},
  journal = {Nucleic acid therapeutics},
  doi = {10.1089/nat.2017.0682},
  url = {https://doi.org/10.1089/nat.2017.0682}
}

RIS

TY  - JOUR
TI  - Development of Exon Skipping Therapies for Duchenne Muscular Dystrophy: A Critical Review and a Perspective on the Outstanding Issues.
AU  - Aartsma-Rus A
AU  - Straub V
AU  - Hemmings R
AU  - Haas M
AU  - Schlosser-Weber G
AU  - Stoyanova-Beninska V
AU  - Mercuri E
AU  - Muntoni F
AU  - Sepodes B
AU  - Vroom E
AU  - Balabanov P
PY  - 2017
JO  - Nucleic acid therapeutics
DO  - 10.1089/nat.2017.0682
UR  - https://doi.org/10.1089/nat.2017.0682
ER  -

APA

A, A., V, S., R, H., M, H., G, S., V, S., E, M., F, M., B, S., E, V., & P, B. (2017). Development of Exon Skipping Therapies for Duchenne Muscular Dystrophy: A Critical Review and a Perspective on the Outstanding Issues.. Nucleic acid therapeutics. https://doi.org/10.1089/nat.2017.0682

Source records

pubmed · retrieved 2026-09-27T12:06:06.084Z