Angelman syndrome patient-derived neuron screen leads to clinical ASO rugonersen targeting UBE3A-ATS with long-lasting effect in monkeys.
- DOI
- 10.1093/nar/gkaf851
- Published
- 2025 Aug 27
- Container
- Nucleic acids research
- Publisher
- Not recorded
- Open access
- yes
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Cite this work
BibTeX
@article{allodium:10.1093/nar/gkaf851,
title = {Angelman syndrome patient-derived neuron screen leads to clinical ASO rugonersen targeting UBE3A-ATS with long-lasting effect in monkeys.},
author = {Jagasia R and Bon C and Rasmussen SV and Badillo S and Tehler D and Buchy D and Berrera M and Prasad M and Chamberlain S and Terrigno M and Pandya NJ and Costa V and Wang C and Pedersen L and Miller MT and Erichsen KD and Joenson L and Patsch C and Hipp JF and Bonni A and Müller L and Braendli-Baiocco A and Kremer T and Koller E and Hoener MC},
year = {2025},
journal = {Nucleic acids research},
doi = {10.1093/nar/gkaf851},
url = {https://doi.org/10.1093/nar/gkaf851}
}RIS
TY - JOUR TI - Angelman syndrome patient-derived neuron screen leads to clinical ASO rugonersen targeting UBE3A-ATS with long-lasting effect in monkeys. AU - Jagasia R AU - Bon C AU - Rasmussen SV AU - Badillo S AU - Tehler D AU - Buchy D AU - Berrera M AU - Prasad M AU - Chamberlain S AU - Terrigno M AU - Pandya NJ AU - Costa V AU - Wang C AU - Pedersen L AU - Miller MT AU - Erichsen KD AU - Joenson L AU - Patsch C AU - Hipp JF AU - Bonni A AU - Müller L AU - Braendli-Baiocco A AU - Kremer T AU - Koller E AU - Hoener MC PY - 2025 JO - Nucleic acids research DO - 10.1093/nar/gkaf851 UR - https://doi.org/10.1093/nar/gkaf851 ER -
APA
R, J., C, B., SV, R., S, B., D, T., D, B., M, B., M, P., S, C., M, T., NJ, P., V, C., C, W., L, P., MT, M., KD, E., L, J., C, P., JF, H., A, B., L, M., A, B., T, K., E, K., & MC, H. (2025). Angelman syndrome patient-derived neuron screen leads to clinical ASO rugonersen targeting UBE3A-ATS with long-lasting effect in monkeys.. Nucleic acids research. https://doi.org/10.1093/nar/gkaf851
Source records
- pubmed · retrieved 2026-09-26T06:48:26.141Z