How Does Hematopoietic Stem Cell Gene Therapy Affect Hip Dysplasia in Mucopolysaccharidosis Type I Hurler Syndrome? Radiological Outcomes at a Minimum 4-year Follow-up

Maurizio De Pellegrin, Matilde Cossutta, Giulia Consiglieri, Francesca Contisciani, Chiara Filisetti, Francesca Tucci, Camilla Morosini, Renata Mellone, Simone Romeni, Alessandro Aiuti, Maria Ester Bernardo

Open source

DOI
10.1097/corr.0000000000004183
Published
2026-11-03
Container
Clinical Orthopaedics & Related Research
Publisher
Ovid Technologies (Wolters Kluwer Health)
Open access
unknown

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BibTeX

@article{allodium:10.1097/corr.0000000000004183,
  title = {How Does Hematopoietic Stem Cell Gene Therapy Affect Hip Dysplasia in Mucopolysaccharidosis Type I Hurler Syndrome? Radiological Outcomes at a Minimum 4-year Follow-up},
  author = {Maurizio De Pellegrin and Matilde Cossutta and Giulia Consiglieri and Francesca Contisciani and Chiara Filisetti and Francesca Tucci and Camilla Morosini and Renata Mellone and Simone Romeni and Alessandro Aiuti and Maria Ester Bernardo},
  year = {2026},
  journal = {Clinical Orthopaedics \& Related Research},
  doi = {10.1097/corr.0000000000004183},
  url = {https://doi.org/10.1097/corr.0000000000004183}
}

RIS

TY  - JOUR
TI  - How Does Hematopoietic Stem Cell Gene Therapy Affect Hip Dysplasia in Mucopolysaccharidosis Type I Hurler Syndrome? Radiological Outcomes at a Minimum 4-year Follow-up
AU  - Maurizio De Pellegrin
AU  - Matilde Cossutta
AU  - Giulia Consiglieri
AU  - Francesca Contisciani
AU  - Chiara Filisetti
AU  - Francesca Tucci
AU  - Camilla Morosini
AU  - Renata Mellone
AU  - Simone Romeni
AU  - Alessandro Aiuti
AU  - Maria Ester Bernardo
PY  - 2026
JO  - Clinical Orthopaedics & Related Research
DO  - 10.1097/corr.0000000000004183
UR  - https://doi.org/10.1097/corr.0000000000004183
ER  - 

APA

Pellegrin, M. D., Cossutta, M., Consiglieri, G., Contisciani, F., Filisetti, C., Tucci, F., Morosini, C., Mellone, R., Romeni, S., Aiuti, A., & Bernardo, M. E. (2026). How Does Hematopoietic Stem Cell Gene Therapy Affect Hip Dysplasia in Mucopolysaccharidosis Type I Hurler Syndrome? Radiological Outcomes at a Minimum 4-year Follow-up. Clinical Orthopaedics & Related Research. https://doi.org/10.1097/corr.0000000000004183

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