Population Pharmacokinetic Modeling and Determination of Individual Exposure to Avalglucosidase Alfa in Adolescent and Adult Patients With Late-Onset Pompe Disease: Analysis of Pooled Data From Phase I to III Clinical Trials.
- DOI
- 10.1097/ftd.0000000000001086
- Published
- 2023 Oct 1
- Container
- Therapeutic drug monitoring
- Publisher
- Not recorded
- Open access
- yes
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Cite this work
BibTeX
@article{allodium:10.1097/ftd.0000000000001086,
title = {Population Pharmacokinetic Modeling and Determination of Individual Exposure to Avalglucosidase Alfa in Adolescent and Adult Patients With Late-Onset Pompe Disease: Analysis of Pooled Data From Phase I to III Clinical Trials.},
author = {Tuffal G and Tiraboschi G and Hurbin F and Boittet P and Palmer R and Martinez JM and Fabre D},
year = {2023},
journal = {Therapeutic drug monitoring},
doi = {10.1097/ftd.0000000000001086},
url = {https://doi.org/10.1097/ftd.0000000000001086}
}RIS
TY - JOUR TI - Population Pharmacokinetic Modeling and Determination of Individual Exposure to Avalglucosidase Alfa in Adolescent and Adult Patients With Late-Onset Pompe Disease: Analysis of Pooled Data From Phase I to III Clinical Trials. AU - Tuffal G AU - Tiraboschi G AU - Hurbin F AU - Boittet P AU - Palmer R AU - Martinez JM AU - Fabre D PY - 2023 JO - Therapeutic drug monitoring DO - 10.1097/ftd.0000000000001086 UR - https://doi.org/10.1097/ftd.0000000000001086 ER -
APA
G, T., G, T., F, H., P, B., R, P., JM, M., & D, F. (2023). Population Pharmacokinetic Modeling and Determination of Individual Exposure to Avalglucosidase Alfa in Adolescent and Adult Patients With Late-Onset Pompe Disease: Analysis of Pooled Data From Phase I to III Clinical Trials.. Therapeutic drug monitoring. https://doi.org/10.1097/ftd.0000000000001086
Source records
- pubmed · retrieved 2026-09-26T10:12:03.077Z
- europe-pmc · retrieved 2026-09-26T10:12:03.095Z