Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA.

Hansen BE, Vandriel SM, Vig P, Garner W, Mogul DB, Loomes KM, Piccoli DA, Rand EB, Jankowska I, Czubkowski P, Gliwicz-Miedzińska D, Gonzales EM, Jacquemin E, Bouligand J, D'Antiga L, Nicastro E, Arnell H, Fischler B, Sokal É, Demaret T, Siew S, Stormon M, Karpen SJ, Romero R, Ebel NH, Feinstein JA, Roberts AJ, Evans HM, Sundaram SS, Chaidez A, Hardikar W, Shankar S, Fischer RT, Lacaille F, Debray D, Lin HC, Jensen MK, Jaramillo C, Karthikeyan P, Indolfi G, Verkade HJ, Larson-Nath C, Quiros-Tejeira RE, Valentino PL, Rogalidou M, Dezsőfi A, Squires JE, Schwarz K, Calvo PL, Bernabeu JQ, Zizzo AN, Nebbia G, Bulut P, Santos-Silva E, Fawaz R, Nastasio S, Karnsakul W, Tamara ML, Busoms CM, Kelly DA, Sandahl TD, Jimenez-Rivera C, Banales JM, Mujawar Q, Li LT, She H, Wang JS, Kim KM, Oh SH, Sanchez MC, Cavalieri ML, Lee WS, Hajinicolaou C, Lertudomphonwanit C, Waisbourd-Zinman O, Arikan C, Alam S, Carvalho E, Melere M, Eshun J, Önal Z, Desai DM, Wiecek S, Pinto RB, Wolters VM, Garcia J, Beretta M, Kerkar N, Brecelj J, Rock N, Lurz E, Blondet N, Shah U, Thompson RJ, Kamath BM, Global ALagille Alliance (GALA) Study Group

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DOI: 10.1097/hep.0000000000000727
Published: 2024 Jun 1
Container: Hepatology (Baltimore, Md.)
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1097/hep.0000000000000727,
  title = {Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA.},
  author = {Hansen BE and Vandriel SM and Vig P and Garner W and Mogul DB and Loomes KM and Piccoli DA and Rand EB and Jankowska I and Czubkowski P and Gliwicz-Miedzińska D and Gonzales EM and Jacquemin E and Bouligand J and D'Antiga L and Nicastro E and Arnell H and Fischler B and Sokal É and Demaret T and Siew S and Stormon M and Karpen SJ and Romero R and Ebel NH and Feinstein JA and Roberts AJ and Evans HM and Sundaram SS and Chaidez A and Hardikar W and Shankar S and Fischer RT and Lacaille F and Debray D and Lin HC and Jensen MK and Jaramillo C and Karthikeyan P and Indolfi G and Verkade HJ and Larson-Nath C and Quiros-Tejeira RE and Valentino PL and Rogalidou M and Dezsőfi A and Squires JE and Schwarz K and Calvo PL and Bernabeu JQ and Zizzo AN and Nebbia G and Bulut P and Santos-Silva E and Fawaz R and Nastasio S and Karnsakul W and Tamara ML and Busoms CM and Kelly DA and Sandahl TD and Jimenez-Rivera C and Banales JM and Mujawar Q and Li LT and She H and Wang JS and Kim KM and Oh SH and Sanchez MC and Cavalieri ML and Lee WS and Hajinicolaou C and Lertudomphonwanit C and Waisbourd-Zinman O and Arikan C and Alam S and Carvalho E and Melere M and Eshun J and Önal Z and Desai DM and Wiecek S and Pinto RB and Wolters VM and Garcia J and Beretta M and Kerkar N and Brecelj J and Rock N and Lurz E and Blondet N and Shah U and Thompson RJ and Kamath BM and Global ALagille Alliance (GALA) Study Group},
  year = {2024},
  journal = {Hepatology (Baltimore, Md.)},
  doi = {10.1097/hep.0000000000000727},
  url = {https://doi.org/10.1097/hep.0000000000000727}
}

RIS

TY  - JOUR
TI  - Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA.
AU  - Hansen BE
AU  - Vandriel SM
AU  - Vig P
AU  - Garner W
AU  - Mogul DB
AU  - Loomes KM
AU  - Piccoli DA
AU  - Rand EB
AU  - Jankowska I
AU  - Czubkowski P
AU  - Gliwicz-Miedzińska D
AU  - Gonzales EM
AU  - Jacquemin E
AU  - Bouligand J
AU  - D'Antiga L
AU  - Nicastro E
AU  - Arnell H
AU  - Fischler B
AU  - Sokal É
AU  - Demaret T
AU  - Siew S
AU  - Stormon M
AU  - Karpen SJ
AU  - Romero R
AU  - Ebel NH
AU  - Feinstein JA
AU  - Roberts AJ
AU  - Evans HM
AU  - Sundaram SS
AU  - Chaidez A
AU  - Hardikar W
AU  - Shankar S
AU  - Fischer RT
AU  - Lacaille F
AU  - Debray D
AU  - Lin HC
AU  - Jensen MK
AU  - Jaramillo C
AU  - Karthikeyan P
AU  - Indolfi G
AU  - Verkade HJ
AU  - Larson-Nath C
AU  - Quiros-Tejeira RE
AU  - Valentino PL
AU  - Rogalidou M
AU  - Dezsőfi A
AU  - Squires JE
AU  - Schwarz K
AU  - Calvo PL
AU  - Bernabeu JQ
AU  - Zizzo AN
AU  - Nebbia G
AU  - Bulut P
AU  - Santos-Silva E
AU  - Fawaz R
AU  - Nastasio S
AU  - Karnsakul W
AU  - Tamara ML
AU  - Busoms CM
AU  - Kelly DA
AU  - Sandahl TD
AU  - Jimenez-Rivera C
AU  - Banales JM
AU  - Mujawar Q
AU  - Li LT
AU  - She H
AU  - Wang JS
AU  - Kim KM
AU  - Oh SH
AU  - Sanchez MC
AU  - Cavalieri ML
AU  - Lee WS
AU  - Hajinicolaou C
AU  - Lertudomphonwanit C
AU  - Waisbourd-Zinman O
AU  - Arikan C
AU  - Alam S
AU  - Carvalho E
AU  - Melere M
AU  - Eshun J
AU  - Önal Z
AU  - Desai DM
AU  - Wiecek S
AU  - Pinto RB
AU  - Wolters VM
AU  - Garcia J
AU  - Beretta M
AU  - Kerkar N
AU  - Brecelj J
AU  - Rock N
AU  - Lurz E
AU  - Blondet N
AU  - Shah U
AU  - Thompson RJ
AU  - Kamath BM
AU  - Global ALagille Alliance (GALA) Study Group
PY  - 2024
JO  - Hepatology (Baltimore, Md.)
DO  - 10.1097/hep.0000000000000727
UR  - https://doi.org/10.1097/hep.0000000000000727
ER  -

APA

BE, H., SM, V., P, V., W, G., DB, M., KM, L., DA, P., EB, R., I, J., P, C., D, G., EM, G., E, J., J, B., L, D., E, N., H, A., B, F., É, S., T, D., S, S., M, S., SJ, K., R, R., NH, E., JA, F., AJ, R., HM, E., SS, S., A, C., W, H., S, S., RT, F., F, L., D, D., HC, L., MK, J., C, J., P, K., G, I., HJ, V., C, L., RE, Q., PL, V., M, R., A, D., JE, S., K, S., PL, C., JQ, B., AN, Z., G, N., P, B., E, S., R, F., S, N., W, K., ML, T., CM, B., DA, K., TD, S., C, J., JM, B., Q, M., LT, L., H, S., JS, W., KM, K., SH, O., MC, S., ML, C., WS, L., C, H., C, L., O, W., C, A., S, A., E, C., M, M., J, E., Z, Ö., DM, D., S, W., RB, P., VM, W., J, G., M, B., N, K., J, B., N, R., E, L., N, B., U, S., RJ, T., BM, K., & Group, G. A. A. (. S. (2024). Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA.. Hepatology (Baltimore, Md.). https://doi.org/10.1097/hep.0000000000000727

Source records

pubmed · retrieved 2026-09-26T15:27:00.518Z