Targeted long-read RNA sequencing for rare disease diagnosis and variant interpretation.

Wang R, Wang F, DeBruyne N, Ji X, Engelhardt NM, Park JJ, Notaro A, Gaerlan S, Park R, Schultz MJ, Clever S, McCormick EM, Keith K, Ng BG, Kadash-Edmondson KE, Freeze HH, Lam CT, Morava E, Helbig I, Falk MJ, Ganetzky RD, Edmondson AC, Lin L, Xing Y

Open source

DOI
10.1126/sciadv.ady9895
Published
2026 Apr 17
Container
Science advances
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1126/sciadv.ady9895,
  title = {Targeted long-read RNA sequencing for rare disease diagnosis and variant interpretation.},
  author = {Wang R and Wang F and DeBruyne N and Ji X and Engelhardt NM and Park JJ and Notaro A and Gaerlan S and Park R and Schultz MJ and Clever S and McCormick EM and Keith K and Ng BG and Kadash-Edmondson KE and Freeze HH and Lam CT and Morava E and Helbig I and Falk MJ and Ganetzky RD and Edmondson AC and Lin L and Xing Y},
  year = {2026},
  journal = {Science advances},
  doi = {10.1126/sciadv.ady9895},
  url = {https://doi.org/10.1126/sciadv.ady9895}
}

RIS

TY  - JOUR
TI  - Targeted long-read RNA sequencing for rare disease diagnosis and variant interpretation.
AU  - Wang R
AU  - Wang F
AU  - DeBruyne N
AU  - Ji X
AU  - Engelhardt NM
AU  - Park JJ
AU  - Notaro A
AU  - Gaerlan S
AU  - Park R
AU  - Schultz MJ
AU  - Clever S
AU  - McCormick EM
AU  - Keith K
AU  - Ng BG
AU  - Kadash-Edmondson KE
AU  - Freeze HH
AU  - Lam CT
AU  - Morava E
AU  - Helbig I
AU  - Falk MJ
AU  - Ganetzky RD
AU  - Edmondson AC
AU  - Lin L
AU  - Xing Y
PY  - 2026
JO  - Science advances
DO  - 10.1126/sciadv.ady9895
UR  - https://doi.org/10.1126/sciadv.ady9895
ER  - 

APA

R, W., F, W., N, D., X, J., NM, E., JJ, P., A, N., S, G., R, P., MJ, S., S, C., EM, M., K, K., BG, N., KE, K., HH, F., CT, L., E, M., I, H., MJ, F., RD, G., AC, E., L, L., & Y, X. (2026). Targeted long-read RNA sequencing for rare disease diagnosis and variant interpretation.. Science advances. https://doi.org/10.1126/sciadv.ady9895

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