Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity.

Braun CJ, Boztug K, Paruzynski A, Witzel M, Schwarzer A, Rothe M, Modlich U, Beier R, Göhring G, Steinemann D, Fronza R, Ball CR, Haemmerle R, Naundorf S, Kühlcke K, Rose M, Fraser C, Mathias L, Ferrari R, Abboud MR, Al-Herz W, Kondratenko I, Maródi L, Glimm H, Schlegelberger B, Schambach A, Albert MH, Schmidt M, von Kalle C, Klein C

Open source

DOI: 10.1126/scitranslmed.3007280
Published: 2014 Mar 12
Container: Science translational medicine
Publisher: Not recorded
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1126/scitranslmed.3007280,
  title = {Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity.},
  author = {Braun CJ and Boztug K and Paruzynski A and Witzel M and Schwarzer A and Rothe M and Modlich U and Beier R and Göhring G and Steinemann D and Fronza R and Ball CR and Haemmerle R and Naundorf S and Kühlcke K and Rose M and Fraser C and Mathias L and Ferrari R and Abboud MR and Al-Herz W and Kondratenko I and Maródi L and Glimm H and Schlegelberger B and Schambach A and Albert MH and Schmidt M and von Kalle C and Klein C},
  year = {2014},
  journal = {Science translational medicine},
  doi = {10.1126/scitranslmed.3007280},
  url = {https://doi.org/10.1126/scitranslmed.3007280}
}

RIS

TY  - JOUR
TI  - Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity.
AU  - Braun CJ
AU  - Boztug K
AU  - Paruzynski A
AU  - Witzel M
AU  - Schwarzer A
AU  - Rothe M
AU  - Modlich U
AU  - Beier R
AU  - Göhring G
AU  - Steinemann D
AU  - Fronza R
AU  - Ball CR
AU  - Haemmerle R
AU  - Naundorf S
AU  - Kühlcke K
AU  - Rose M
AU  - Fraser C
AU  - Mathias L
AU  - Ferrari R
AU  - Abboud MR
AU  - Al-Herz W
AU  - Kondratenko I
AU  - Maródi L
AU  - Glimm H
AU  - Schlegelberger B
AU  - Schambach A
AU  - Albert MH
AU  - Schmidt M
AU  - von Kalle C
AU  - Klein C
PY  - 2014
JO  - Science translational medicine
DO  - 10.1126/scitranslmed.3007280
UR  - https://doi.org/10.1126/scitranslmed.3007280
ER  -

APA

CJ, B., K, B., A, P., M, W., A, S., M, R., U, M., R, B., G, G., D, S., R, F., CR, B., R, H., S, N., K, K., M, R., C, F., L, M., R, F., MR, A., W, A., I, K., L, M., H, G., B, S., A, S., MH, A., M, S., C, V. K., & C, K. (2014). Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity.. Science translational medicine. https://doi.org/10.1126/scitranslmed.3007280

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pubmed · retrieved 2026-09-25T08:13:45.106Z