High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease.

Bzhilyanskaya V, Ma L, Liu S, Fox LR, Whittaker MN, Meis RJ, Choi U, Lawson A, Ma M, Theobald N, Burkett S, Sweeney CL, Lazzarotto CR, Tsai SQ, Lack JB, Wu X, Dahl GA, Malech HL, Kleinstiver BP, De Ravin SS

Open source

DOI: 10.1126/scitranslmed.adj6779
Published: 2024 Oct 16
Container: Science translational medicine
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1126/scitranslmed.adj6779,
  title = {High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease.},
  author = {Bzhilyanskaya V and Ma L and Liu S and Fox LR and Whittaker MN and Meis RJ and Choi U and Lawson A and Ma M and Theobald N and Burkett S and Sweeney CL and Lazzarotto CR and Tsai SQ and Lack JB and Wu X and Dahl GA and Malech HL and Kleinstiver BP and De Ravin SS},
  year = {2024},
  journal = {Science translational medicine},
  doi = {10.1126/scitranslmed.adj6779},
  url = {https://doi.org/10.1126/scitranslmed.adj6779}
}

RIS

TY  - JOUR
TI  - High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease.
AU  - Bzhilyanskaya V
AU  - Ma L
AU  - Liu S
AU  - Fox LR
AU  - Whittaker MN
AU  - Meis RJ
AU  - Choi U
AU  - Lawson A
AU  - Ma M
AU  - Theobald N
AU  - Burkett S
AU  - Sweeney CL
AU  - Lazzarotto CR
AU  - Tsai SQ
AU  - Lack JB
AU  - Wu X
AU  - Dahl GA
AU  - Malech HL
AU  - Kleinstiver BP
AU  - De Ravin SS
PY  - 2024
JO  - Science translational medicine
DO  - 10.1126/scitranslmed.adj6779
UR  - https://doi.org/10.1126/scitranslmed.adj6779
ER  -

APA

V, B., L, M., S, L., LR, F., MN, W., RJ, M., U, C., A, L., M, M., N, T., S, B., CL, S., CR, L., SQ, T., JB, L., X, W., GA, D., HL, M., BP, K., & SS, D. R. (2024). High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease.. Science translational medicine. https://doi.org/10.1126/scitranslmed.adj6779

Source records

pubmed · retrieved 2026-09-27T00:33:51.950Z