RNA-LNP-mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I.

Tálas A, Ioannidi EI, Weber Y, Haenggi T, Kulcsár PI, Zürcher N, Faccin E, Moon WJ, Kissling L, Villiger EA, Matsushita M, Rothgangl T, Janjuha S, Lin PJC, Poms M, Muramatsu H, Vadovics M, Reichmuth A, Kopf M, Pardi N, Tam YK, Häberle J, Schwank G

Open source

DOI: 10.1126/scitranslmed.aec7274
Published: 2026 May 13
Container: Science translational medicine
Publisher: Not recorded
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1126/scitranslmed.aec7274,
  title = {RNA-LNP-mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I.},
  author = {Tálas A and Ioannidi EI and Weber Y and Haenggi T and Kulcsár PI and Zürcher N and Faccin E and Moon WJ and Kissling L and Villiger EA and Matsushita M and Rothgangl T and Janjuha S and Lin PJC and Poms M and Muramatsu H and Vadovics M and Reichmuth A and Kopf M and Pardi N and Tam YK and Häberle J and Schwank G},
  year = {2026},
  journal = {Science translational medicine},
  doi = {10.1126/scitranslmed.aec7274},
  url = {https://doi.org/10.1126/scitranslmed.aec7274}
}

RIS

TY  - JOUR
TI  - RNA-LNP-mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I.
AU  - Tálas A
AU  - Ioannidi EI
AU  - Weber Y
AU  - Haenggi T
AU  - Kulcsár PI
AU  - Zürcher N
AU  - Faccin E
AU  - Moon WJ
AU  - Kissling L
AU  - Villiger EA
AU  - Matsushita M
AU  - Rothgangl T
AU  - Janjuha S
AU  - Lin PJC
AU  - Poms M
AU  - Muramatsu H
AU  - Vadovics M
AU  - Reichmuth A
AU  - Kopf M
AU  - Pardi N
AU  - Tam YK
AU  - Häberle J
AU  - Schwank G
PY  - 2026
JO  - Science translational medicine
DO  - 10.1126/scitranslmed.aec7274
UR  - https://doi.org/10.1126/scitranslmed.aec7274
ER  -

APA

A, T., EI, I., Y, W., T, H., PI, K., N, Z., E, F., WJ, M., L, K., EA, V., M, M., T, R., S, J., PJC, L., M, P., H, M., M, V., A, R., M, K., N, P., YK, T., J, H., & G, S. (2026). RNA-LNP-mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I.. Science translational medicine. https://doi.org/10.1126/scitranslmed.aec7274

Source records

pubmed · retrieved 2026-09-25T00:39:54.599Z