Global insight into rare disease and orphan drug definitions: a systematic literature review.

Abozaid GM, Kerr K, Alomary H, Al-Omar HA, McKnight A

DOI: 10.1136/bmjopen-2024-086527
Published: 2025 Jan 25
Container: BMJ open
Publisher: Not recorded
Open access: yes

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limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

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Cite this work

BibTeX

@article{allodium:10.1136/bmjopen-2024-086527,
  title = {Global insight into rare disease and orphan drug definitions: a systematic literature review.},
  author = {Abozaid GM and Kerr K and Alomary H and Al-Omar HA and McKnight A},
  year = {2025},
  journal = {BMJ open},
  doi = {10.1136/bmjopen-2024-086527},
  url = {https://doi.org/10.1136/bmjopen-2024-086527}
}

RIS

TY  - JOUR
TI  - Global insight into rare disease and orphan drug definitions: a systematic literature review.
AU  - Abozaid GM
AU  - Kerr K
AU  - Alomary H
AU  - Al-Omar HA
AU  - McKnight A
PY  - 2025
JO  - BMJ open
DO  - 10.1136/bmjopen-2024-086527
UR  - https://doi.org/10.1136/bmjopen-2024-086527
ER  -

APA

GM, A., K, K., H, A., HA, A., & A, M. (2025). Global insight into rare disease and orphan drug definitions: a systematic literature review.. BMJ open. https://doi.org/10.1136/bmjopen-2024-086527

Source records

pubmed · retrieved 2026-09-26T11:10:33.660Z