Gene-Corrected Human iPSC-Derived Cardiomyocytes and Skeletal Muscles Reveal Partial Dystrophin Dp427 Preservation and Cardiac Dp116 Expression in Duchenne Muscular Dystrophy Patient With a Splice-Site Mutation in Intron 68 (c.9975-1G>T).

Białobrzeska M, Przymuszała M, Ferdek P, Viestia I, Potulska-Chromik A, Kostera-Pruszczyk A, Łuczak-Woźniak K, Stępniewski J, Florczyk-Soluch U, Dulak J

Open source

DOI
10.1161/circgen.125.005376
Published
2026 Sep 25
Container
Circulation. Genomic and precision medicine
Publisher
Not recorded
Open access
unknown

Credibility signals

limited evidence Score 43/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.1161/circgen.125.005376,
  title = {Gene-Corrected Human iPSC-Derived Cardiomyocytes and Skeletal Muscles Reveal Partial Dystrophin Dp427 Preservation and Cardiac Dp116 Expression in Duchenne Muscular Dystrophy Patient With a Splice-Site Mutation in Intron 68 (c.9975-1G>T).},
  author = {Białobrzeska M and Przymuszała M and Ferdek P and Viestia I and Potulska-Chromik A and Kostera-Pruszczyk A and Łuczak-Woźniak K and Stępniewski J and Florczyk-Soluch U and Dulak J},
  year = {2026},
  journal = {Circulation. Genomic and precision medicine},
  doi = {10.1161/circgen.125.005376},
  url = {https://doi.org/10.1161/circgen.125.005376}
}

RIS

TY  - JOUR
TI  - Gene-Corrected Human iPSC-Derived Cardiomyocytes and Skeletal Muscles Reveal Partial Dystrophin Dp427 Preservation and Cardiac Dp116 Expression in Duchenne Muscular Dystrophy Patient With a Splice-Site Mutation in Intron 68 (c.9975-1G>T).
AU  - Białobrzeska M
AU  - Przymuszała M
AU  - Ferdek P
AU  - Viestia I
AU  - Potulska-Chromik A
AU  - Kostera-Pruszczyk A
AU  - Łuczak-Woźniak K
AU  - Stępniewski J
AU  - Florczyk-Soluch U
AU  - Dulak J
PY  - 2026
JO  - Circulation. Genomic and precision medicine
DO  - 10.1161/circgen.125.005376
UR  - https://doi.org/10.1161/circgen.125.005376
ER  - 

APA

M, B., M, P., P, F., I, V., A, P., A, K., K, Ł., J, S., U, F., & J, D. (2026). Gene-Corrected Human iPSC-Derived Cardiomyocytes and Skeletal Muscles Reveal Partial Dystrophin Dp427 Preservation and Cardiac Dp116 Expression in Duchenne Muscular Dystrophy Patient With a Splice-Site Mutation in Intron 68 (c.9975-1G>T).. Circulation. Genomic and precision medicine. https://doi.org/10.1161/circgen.125.005376

Source records