Phase III trial of sodium dichloroacetate for pyruvate dehydrogenase complex deficiency in children

Peter W. Stacpoole, Jose E. Abdenur, Jirair K. Bedoyan, Lorenzo Botto, Gregory M. Enns, Marni J. Falk, Rebecca Ganetzky, Cheryl Garganta, Kevin Glinton, Andrea Gropman, Sharon Hamm, Eugenia Henry, Nicola Longo, Richard Neiberger, Russell P. Saneto, Fernando Scaglia, Sub H. Subramony, Jerry Vockley, Richard E. Wagner

Open source

DOI: 10.1172/jci.insight.200149
Published: 2026-09-22
Container: JCI Insight
Publisher: American Society for Clinical Investigation
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1172/jci.insight.200149,
  title = {Phase III trial of sodium dichloroacetate for pyruvate dehydrogenase complex deficiency in children},
  author = {Peter W. Stacpoole and Jose E. Abdenur and Jirair K. Bedoyan and Lorenzo Botto and Gregory M. Enns and Marni J. Falk and Rebecca Ganetzky and Cheryl Garganta and Kevin Glinton and Andrea Gropman and Sharon Hamm and Eugenia Henry and Nicola Longo and Richard Neiberger and Russell P. Saneto and Fernando Scaglia and Sub H. Subramony and Jerry Vockley and Richard E. Wagner},
  year = {2026},
  journal = {JCI Insight},
  doi = {10.1172/jci.insight.200149},
  url = {https://doi.org/10.1172/jci.insight.200149}
}

RIS

TY  - JOUR
TI  - Phase III trial of sodium dichloroacetate for pyruvate dehydrogenase complex deficiency in children
AU  - Peter W. Stacpoole
AU  - Jose E. Abdenur
AU  - Jirair K. Bedoyan
AU  - Lorenzo Botto
AU  - Gregory M. Enns
AU  - Marni J. Falk
AU  - Rebecca Ganetzky
AU  - Cheryl Garganta
AU  - Kevin Glinton
AU  - Andrea Gropman
AU  - Sharon Hamm
AU  - Eugenia Henry
AU  - Nicola Longo
AU  - Richard Neiberger
AU  - Russell P. Saneto
AU  - Fernando Scaglia
AU  - Sub H. Subramony
AU  - Jerry Vockley
AU  - Richard E. Wagner
PY  - 2026
JO  - JCI Insight
DO  - 10.1172/jci.insight.200149
UR  - https://doi.org/10.1172/jci.insight.200149
ER  -

APA

Stacpoole, P. W., Abdenur, J. E., Bedoyan, J. K., Botto, L., Enns, G. M., Falk, M. J., Ganetzky, R., Garganta, C., Glinton, K., Gropman, A., Hamm, S., Henry, E., Longo, N., Neiberger, R., Saneto, R. P., Scaglia, F., Subramony, S. H., Vockley, J., & Wagner, R. E. (2026). Phase III trial of sodium dichloroacetate for pyruvate dehydrogenase complex deficiency in children. JCI Insight. https://doi.org/10.1172/jci.insight.200149

Source records

crossref · retrieved 2026-09-25T08:13:57.082Z