Targeted gene therapy alleviates epilepsy and hyperexcitability in models of SCN2A deficiency

Zaiyang Zhang, Jingliang Zhang, Xiaoling Chen, Brody A. Deming, Shivam Kant, Purba Mandal, Harish Kothandaraman, Phillip J. SanMiguel, Manasi S. Halurkar, Akila D. Abeyaratna, Morgan J. Robinson, Iuliia Vitko, Ronald P. Gaykema, Chongli Yuan, Nadia A. Lanman, Matthew T. Tegtmeyer, Dan Wang, Guangping Gao, Riyi Shi, Edward Perez-Reyes, Yang Yang

Open source

DOI
10.1172/jci196068
Published
2026-11-03
Container
Journal of Clinical Investigation
Publisher
American Society for Clinical Investigation
Open access
unknown

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BibTeX

@article{allodium:10.1172/jci196068,
  title = {Targeted gene therapy alleviates epilepsy and hyperexcitability in models of SCN2A deficiency},
  author = {Zaiyang Zhang and Jingliang Zhang and Xiaoling Chen and Brody A. Deming and Shivam Kant and Purba Mandal and Harish Kothandaraman and Phillip J. SanMiguel and Manasi S. Halurkar and Akila D. Abeyaratna and Morgan J. Robinson and Iuliia Vitko and Ronald P. Gaykema and Chongli Yuan and Nadia A. Lanman and Matthew T. Tegtmeyer and Dan Wang and Guangping Gao and Riyi Shi and Edward Perez-Reyes and Yang Yang},
  year = {2026},
  journal = {Journal of Clinical Investigation},
  doi = {10.1172/jci196068},
  url = {https://doi.org/10.1172/jci196068}
}

RIS

TY  - JOUR
TI  - Targeted gene therapy alleviates epilepsy and hyperexcitability in models of SCN2A deficiency
AU  - Zaiyang Zhang
AU  - Jingliang Zhang
AU  - Xiaoling Chen
AU  - Brody A. Deming
AU  - Shivam Kant
AU  - Purba Mandal
AU  - Harish Kothandaraman
AU  - Phillip J. SanMiguel
AU  - Manasi S. Halurkar
AU  - Akila D. Abeyaratna
AU  - Morgan J. Robinson
AU  - Iuliia Vitko
AU  - Ronald P. Gaykema
AU  - Chongli Yuan
AU  - Nadia A. Lanman
AU  - Matthew T. Tegtmeyer
AU  - Dan Wang
AU  - Guangping Gao
AU  - Riyi Shi
AU  - Edward Perez-Reyes
AU  - Yang Yang
PY  - 2026
JO  - Journal of Clinical Investigation
DO  - 10.1172/jci196068
UR  - https://doi.org/10.1172/jci196068
ER  - 

APA

Zhang, Z., Zhang, J., Chen, X., Deming, B. A., Kant, S., Mandal, P., Kothandaraman, H., SanMiguel, P. J., Halurkar, M. S., Abeyaratna, A. D., Robinson, M. J., Vitko, I., Gaykema, R. P., Yuan, C., Lanman, N. A., Tegtmeyer, M. T., Wang, D., Gao, G., Shi, R., Perez-Reyes, E., & Yang, Y. (2026). Targeted gene therapy alleviates epilepsy and hyperexcitability in models of SCN2A deficiency. Journal of Clinical Investigation. https://doi.org/10.1172/jci196068

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