Genome Editing for Familial Hemophagocytic Lymphohistiocytosis: Design Principles, Challenges, and Translational Perspectives

Ghazale Minaiyan, Clotilde Aussel, Sandra Ammann, Toni Cathomen

Open source

DOI
10.1177/10430342261465555
Published
2026-07-02
Container
Human Gene Therapy
Publisher
SAGE Publications
Open access
unknown

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BibTeX

@article{allodium:10.1177/10430342261465555,
  title = {Genome Editing for Familial Hemophagocytic Lymphohistiocytosis: Design Principles, Challenges, and Translational Perspectives},
  author = {Ghazale Minaiyan and Clotilde Aussel and Sandra Ammann and Toni Cathomen},
  year = {2026},
  journal = {Human Gene Therapy},
  doi = {10.1177/10430342261465555},
  url = {https://doi.org/10.1177/10430342261465555}
}

RIS

TY  - JOUR
TI  - Genome Editing for Familial Hemophagocytic Lymphohistiocytosis: Design Principles, Challenges, and Translational Perspectives
AU  - Ghazale Minaiyan
AU  - Clotilde Aussel
AU  - Sandra Ammann
AU  - Toni Cathomen
PY  - 2026
JO  - Human Gene Therapy
DO  - 10.1177/10430342261465555
UR  - https://doi.org/10.1177/10430342261465555
ER  - 

APA

Minaiyan, G., Aussel, C., Ammann, S., & Cathomen, T. (2026). Genome Editing for Familial Hemophagocytic Lymphohistiocytosis: Design Principles, Challenges, and Translational Perspectives. Human Gene Therapy. https://doi.org/10.1177/10430342261465555

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