Food and Drug Administration Grants Ultragenyx's Fayuvi™ First-Ever Approval for Sanfilippo Syndrome Type A Treatment.

Philippidis A

DOI: 10.1177/10430342261499483
Published: 2026 Dec
Container: Human gene therapy
Publisher: Not recorded
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1177/10430342261499483,
  title = {Food and Drug Administration Grants Ultragenyx's Fayuvi™ First-Ever Approval for Sanfilippo Syndrome Type A Treatment.},
  author = {Philippidis A},
  year = {2026},
  journal = {Human gene therapy},
  doi = {10.1177/10430342261499483},
  url = {https://doi.org/10.1177/10430342261499483}
}

RIS

TY  - JOUR
TI  - Food and Drug Administration Grants Ultragenyx's Fayuvi™ First-Ever Approval for Sanfilippo Syndrome Type A Treatment.
AU  - Philippidis A
PY  - 2026
JO  - Human gene therapy
DO  - 10.1177/10430342261499483
UR  - https://doi.org/10.1177/10430342261499483
ER  -

APA

A, P. (2026). Food and Drug Administration Grants Ultragenyx's Fayuvi™ First-Ever Approval for Sanfilippo Syndrome Type A Treatment.. Human gene therapy. https://doi.org/10.1177/10430342261499483

Source records

pubmed · retrieved 2026-11-10T13:50:39.631Z