Advances in orphan drug development for alpha-1 antitrypsin deficiency: a 2025 update from the FDA and EMA
- DOI
- 10.1177/17534666251411227
- Published
- 2026-01
- Container
- Therapeutic Advances in Respiratory Disease
- Publisher
- SAGE Publications
- Open access
- unknown
Credibility signals
uncertain Score 64/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- supportingDOI registered: A matching record was returned by Crossref.
- supportingDOI resolves: A matching record was returned by Crossref.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredOpen access status: Not checked or no result supplied; no credibility inference made.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- supportingMetadata completeness: All 6 scored descriptive metadata groups are present.
Cite this work
BibTeX
@article{allodium:10.1177/17534666251411227,
title = {Advances in orphan drug development for alpha-1 antitrypsin deficiency: a 2025 update from the FDA and EMA},
author = {Philipp Höger and Markus Ries and Arturo Olivares Rivera and Hilal Ersöz and Katharina Buschulte and Sebastian Fähndrich and Konstantina Kontogianni and Felix Herth and Franziska C. Trudzinski},
year = {2026},
journal = {Therapeutic Advances in Respiratory Disease},
doi = {10.1177/17534666251411227},
url = {https://doi.org/10.1177/17534666251411227}
}RIS
TY - JOUR TI - Advances in orphan drug development for alpha-1 antitrypsin deficiency: a 2025 update from the FDA and EMA AU - Philipp Höger AU - Markus Ries AU - Arturo Olivares Rivera AU - Hilal Ersöz AU - Katharina Buschulte AU - Sebastian Fähndrich AU - Konstantina Kontogianni AU - Felix Herth AU - Franziska C. Trudzinski PY - 2026 JO - Therapeutic Advances in Respiratory Disease DO - 10.1177/17534666251411227 UR - https://doi.org/10.1177/17534666251411227 ER -
APA
Höger, P., Ries, M., Rivera, A. O., Ersöz, H., Buschulte, K., Fähndrich, S., Kontogianni, K., Herth, F., & Trudzinski, F. C. (2026). Advances in orphan drug development for alpha-1 antitrypsin deficiency: a 2025 update from the FDA and EMA. Therapeutic Advances in Respiratory Disease. https://doi.org/10.1177/17534666251411227
Source records
- crossref · retrieved 2026-09-25T18:16:16.556Z