Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.

Fong S, Swystun LL, Batty P, Lillicrap D

Open source

DOI
10.1177/20406207251406537
Published
2026
Container
Therapeutic advances in hematology
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1177/20406207251406537,
  title = {Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.},
  author = {Fong S and Swystun LL and Batty P and Lillicrap D},
  year = {2026},
  journal = {Therapeutic advances in hematology},
  doi = {10.1177/20406207251406537},
  url = {https://doi.org/10.1177/20406207251406537}
}

RIS

TY  - JOUR
TI  - Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.
AU  - Fong S
AU  - Swystun LL
AU  - Batty P
AU  - Lillicrap D
PY  - 2026
JO  - Therapeutic advances in hematology
DO  - 10.1177/20406207251406537
UR  - https://doi.org/10.1177/20406207251406537
ER  - 

APA

S, F., LL, S., P, B., & D, L. (2026). Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.. Therapeutic advances in hematology. https://doi.org/10.1177/20406207251406537

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