Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence.

Weiß C, Vill K, Baumann M, Bernert G, Blaschek A, Eisenkölbl A, Flotats-Bastardas M, Friese J, Ganter C, Goldhahn K, Hahn A, von der Hagen M, Hartmann H, Hasselmann O, Horber V, Husain RA, Illsinger S, Jacquier D, Johannsen J, Köhler C, Kölbel H, Kolodzig M, Klein A, Pechmann A, von Moers A, Müller-Felber W, Rauscher C, Schara-Schmidt U, Schreiber G, Schwartz O, Sproß J, Stettner GM, Stoltenburg C, Stumpe E, Trollmann R, Wiegand G, Wilichowski E, Kirschner J, Ziegler A, collaborators and members of the INTEGRATE ATMP consortium

Open source

DOI
10.1177/22143602251387019
Published
2026 May
Container
Journal of neuromuscular diseases
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1177/22143602251387019,
  title = {Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence.},
  author = {Weiß C and Vill K and Baumann M and Bernert G and Blaschek A and Eisenkölbl A and Flotats-Bastardas M and Friese J and Ganter C and Goldhahn K and Hahn A and von der Hagen M and Hartmann H and Hasselmann O and Horber V and Husain RA and Illsinger S and Jacquier D and Johannsen J and Köhler C and Kölbel H and Kolodzig M and Klein A and Pechmann A and von Moers A and Müller-Felber W and Rauscher C and Schara-Schmidt U and Schreiber G and Schwartz O and Sproß J and Stettner GM and Stoltenburg C and Stumpe E and Trollmann R and Wiegand G and Wilichowski E and Kirschner J and Ziegler A and collaborators and members of the INTEGRATE ATMP consortium},
  year = {2026},
  journal = {Journal of neuromuscular diseases},
  doi = {10.1177/22143602251387019},
  url = {https://doi.org/10.1177/22143602251387019}
}

RIS

TY  - JOUR
TI  - Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence.
AU  - Weiß C
AU  - Vill K
AU  - Baumann M
AU  - Bernert G
AU  - Blaschek A
AU  - Eisenkölbl A
AU  - Flotats-Bastardas M
AU  - Friese J
AU  - Ganter C
AU  - Goldhahn K
AU  - Hahn A
AU  - von der Hagen M
AU  - Hartmann H
AU  - Hasselmann O
AU  - Horber V
AU  - Husain RA
AU  - Illsinger S
AU  - Jacquier D
AU  - Johannsen J
AU  - Köhler C
AU  - Kölbel H
AU  - Kolodzig M
AU  - Klein A
AU  - Pechmann A
AU  - von Moers A
AU  - Müller-Felber W
AU  - Rauscher C
AU  - Schara-Schmidt U
AU  - Schreiber G
AU  - Schwartz O
AU  - Sproß J
AU  - Stettner GM
AU  - Stoltenburg C
AU  - Stumpe E
AU  - Trollmann R
AU  - Wiegand G
AU  - Wilichowski E
AU  - Kirschner J
AU  - Ziegler A
AU  - collaborators and members of the INTEGRATE ATMP consortium
PY  - 2026
JO  - Journal of neuromuscular diseases
DO  - 10.1177/22143602251387019
UR  - https://doi.org/10.1177/22143602251387019
ER  -

APA

C, W., K, V., M, B., G, B., A, B., A, E., M, F., J, F., C, G., K, G., A, H., M, V. D. H., H, H., O, H., V, H., RA, H., S, I., D, J., J, J., C, K., H, K., M, K., A, K., A, P., A, V. M., W, M., C, R., U, S., G, S., O, S., J, S., GM, S., C, S., E, S., R, T., G, W., E, W., J, K., A, Z., & consortium, C. A. M. O. T. I. A. (2026). Delphi consensus on gene therapy of spinal muscular atrophy with onasemnogene abeparvovec in Germany, Austria and Switzerland-part I-systematic literature review and existing evidence.. Journal of neuromuscular diseases. https://doi.org/10.1177/22143602251387019

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