Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.

Labrosse R, Chu JI, Armant MA, Everett JK, Pellin D, Kareddy N, Frelinger AL, Henderson LA, O'Connell AE, Biswas A, Coenen-van der Spek J, Miggelbrink A, Fiorini C, Adhikari H, Berry CC, Cantu VA, Fong J, Jaroslavsky J, Karadeniz DF, Li QZ, Reddy S, Roche AM, Zhu C, Whangbo JS, Dansereau C, Mackinnon B, Morris E, Koo SM, London WB, Baris S, Ozen A, Karakoc-Aydiner E, Despotovic JM, Forbes Satter LR, Saitoh A, Aizawa Y, King A, Nguyen MAT, Vu VDU, Snapper SB, Galy A, Notarangelo LD, Bushman FD, Williams DA, Pai SY

Open source

DOI: 10.1182/blood.2022019117
Published: 2023 Oct 12
Container: Blood
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1182/blood.2022019117,
  title = {Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.},
  author = {Labrosse R and Chu JI and Armant MA and Everett JK and Pellin D and Kareddy N and Frelinger AL and Henderson LA and O'Connell AE and Biswas A and Coenen-van der Spek J and Miggelbrink A and Fiorini C and Adhikari H and Berry CC and Cantu VA and Fong J and Jaroslavsky J and Karadeniz DF and Li QZ and Reddy S and Roche AM and Zhu C and Whangbo JS and Dansereau C and Mackinnon B and Morris E and Koo SM and London WB and Baris S and Ozen A and Karakoc-Aydiner E and Despotovic JM and Forbes Satter LR and Saitoh A and Aizawa Y and King A and Nguyen MAT and Vu VDU and Snapper SB and Galy A and Notarangelo LD and Bushman FD and Williams DA and Pai SY},
  year = {2023},
  journal = {Blood},
  doi = {10.1182/blood.2022019117},
  url = {https://doi.org/10.1182/blood.2022019117}
}

RIS

TY  - JOUR
TI  - Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.
AU  - Labrosse R
AU  - Chu JI
AU  - Armant MA
AU  - Everett JK
AU  - Pellin D
AU  - Kareddy N
AU  - Frelinger AL
AU  - Henderson LA
AU  - O'Connell AE
AU  - Biswas A
AU  - Coenen-van der Spek J
AU  - Miggelbrink A
AU  - Fiorini C
AU  - Adhikari H
AU  - Berry CC
AU  - Cantu VA
AU  - Fong J
AU  - Jaroslavsky J
AU  - Karadeniz DF
AU  - Li QZ
AU  - Reddy S
AU  - Roche AM
AU  - Zhu C
AU  - Whangbo JS
AU  - Dansereau C
AU  - Mackinnon B
AU  - Morris E
AU  - Koo SM
AU  - London WB
AU  - Baris S
AU  - Ozen A
AU  - Karakoc-Aydiner E
AU  - Despotovic JM
AU  - Forbes Satter LR
AU  - Saitoh A
AU  - Aizawa Y
AU  - King A
AU  - Nguyen MAT
AU  - Vu VDU
AU  - Snapper SB
AU  - Galy A
AU  - Notarangelo LD
AU  - Bushman FD
AU  - Williams DA
AU  - Pai SY
PY  - 2023
JO  - Blood
DO  - 10.1182/blood.2022019117
UR  - https://doi.org/10.1182/blood.2022019117
ER  -

APA

R, L., JI, C., MA, A., JK, E., D, P., N, K., AL, F., LA, H., AE, O., A, B., J, C. D. S., A, M., C, F., H, A., CC, B., VA, C., J, F., J, J., DF, K., QZ, L., S, R., AM, R., C, Z., JS, W., C, D., B, M., E, M., SM, K., WB, L., S, B., A, O., E, K., JM, D., LR, F. S., A, S., Y, A., A, K., MAT, N., VDU, V., SB, S., A, G., LD, N., FD, B., DA, W., & SY, P. (2023). Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.. Blood. https://doi.org/10.1182/blood.2022019117

Source records

pubmed · retrieved 2026-09-26T04:49:43.066Z
europe-pmc · retrieved 2026-09-26T04:49:43.084Z