Therapeutic base editing to generate a gain-of-function <i>F9</i> variant for hemophilia B

Nemekhbayar Baatartsogt, Yuji Kashiwakura, Takafumi Hiramoto, Rina Ito, Rikako Sato, Yasumitsu Nagao, Hina Naruoka, Haruka Takata, Morisada Hayakawa, Khishigjargal Batjargal, Tomoki Togashi, Atsushi Hoshino, Taro Shimizu, Yusuke Sato, Tatsuhiro Ishida, Osamu Nureki, Tsukasa Ohmori

Open source

DOI
10.1182/blood.2024027870
Published
2026-01-22
Container
Blood
Publisher
American Society of Hematology
Open access
unknown

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BibTeX

@article{allodium:10.1182/blood.2024027870,
  title = {Therapeutic base editing to generate a gain-of-function
                    <i>F9</i>
                    variant for hemophilia B},
  author = {Nemekhbayar Baatartsogt and Yuji Kashiwakura and Takafumi Hiramoto and Rina Ito and Rikako Sato and Yasumitsu Nagao and Hina Naruoka and Haruka Takata and Morisada Hayakawa and Khishigjargal Batjargal and Tomoki Togashi and Atsushi Hoshino and Taro Shimizu and Yusuke Sato and Tatsuhiro Ishida and Osamu Nureki and Tsukasa Ohmori},
  year = {2026},
  journal = {Blood},
  doi = {10.1182/blood.2024027870},
  url = {https://doi.org/10.1182/blood.2024027870}
}

RIS

TY  - JOUR
TI  - Therapeutic base editing to generate a gain-of-function
                    <i>F9</i>
                    variant for hemophilia B
AU  - Nemekhbayar Baatartsogt
AU  - Yuji Kashiwakura
AU  - Takafumi Hiramoto
AU  - Rina Ito
AU  - Rikako Sato
AU  - Yasumitsu Nagao
AU  - Hina Naruoka
AU  - Haruka Takata
AU  - Morisada Hayakawa
AU  - Khishigjargal Batjargal
AU  - Tomoki Togashi
AU  - Atsushi Hoshino
AU  - Taro Shimizu
AU  - Yusuke Sato
AU  - Tatsuhiro Ishida
AU  - Osamu Nureki
AU  - Tsukasa Ohmori
PY  - 2026
JO  - Blood
DO  - 10.1182/blood.2024027870
UR  - https://doi.org/10.1182/blood.2024027870
ER  - 

APA

Baatartsogt, N., Kashiwakura, Y., Hiramoto, T., Ito, R., Sato, R., Nagao, Y., Naruoka, H., Takata, H., Hayakawa, M., Batjargal, K., Togashi, T., Hoshino, A., Shimizu, T., Sato, Y., Ishida, T., Nureki, O., & Ohmori, T. (2026). Therapeutic base editing to generate a gain-of-function <i>F9</i> variant for hemophilia B. Blood. https://doi.org/10.1182/blood.2024027870

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