Improvements in health-related quality of life in patients with severe sickle cell disease after exagamglogene autotemcel.

Sharma A, Locatelli F, Bhatia M, Molinari L, Mapara MY, Liem RI, Dedeken L, Wall D, Eckrich MJ, Kuo KHM, Smith W, Imren S, Kohli P, Li N, Liu T, Rubin J, Hobbs W, Grupp SA, Frangoul H

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DOI: 10.1182/bloodadvances.2025016701
Published: 2025 Dec 23
Container: Blood advances
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1182/bloodadvances.2025016701,
  title = {Improvements in health-related quality of life in patients with severe sickle cell disease after exagamglogene autotemcel.},
  author = {Sharma A and Locatelli F and Bhatia M and Molinari L and Mapara MY and Liem RI and Dedeken L and Wall D and Eckrich MJ and Kuo KHM and Smith W and Imren S and Kohli P and Li N and Liu T and Rubin J and Hobbs W and Grupp SA and Frangoul H},
  year = {2025},
  journal = {Blood advances},
  doi = {10.1182/bloodadvances.2025016701},
  url = {https://doi.org/10.1182/bloodadvances.2025016701}
}

RIS

TY  - JOUR
TI  - Improvements in health-related quality of life in patients with severe sickle cell disease after exagamglogene autotemcel.
AU  - Sharma A
AU  - Locatelli F
AU  - Bhatia M
AU  - Molinari L
AU  - Mapara MY
AU  - Liem RI
AU  - Dedeken L
AU  - Wall D
AU  - Eckrich MJ
AU  - Kuo KHM
AU  - Smith W
AU  - Imren S
AU  - Kohli P
AU  - Li N
AU  - Liu T
AU  - Rubin J
AU  - Hobbs W
AU  - Grupp SA
AU  - Frangoul H
PY  - 2025
JO  - Blood advances
DO  - 10.1182/bloodadvances.2025016701
UR  - https://doi.org/10.1182/bloodadvances.2025016701
ER  -

APA

A, S., F, L., M, B., L, M., MY, M., RI, L., L, D., D, W., MJ, E., KHM, K., W, S., S, I., P, K., N, L., T, L., J, R., W, H., SA, G., & H, F. (2025). Improvements in health-related quality of life in patients with severe sickle cell disease after exagamglogene autotemcel.. Blood advances. https://doi.org/10.1182/bloodadvances.2025016701

Source records

pubmed · retrieved 2026-09-27T08:37:31.296Z