Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel

Josu de la Fuente, Haydar Frangoul, Peter Lang, Donna Wall, Roland Meisel, Selim Corbacioglu, Amanda M. Li, Ami J. Shah, Ben Carpenter, Janet L. Kwiatkowski, Markus Y. Mapara, Robert I. Liem, Joachim Rupprecht, Kevin H.M. Kuo, Hayley Merkeley, Mattia Algeri, Wally Smith, Puja Kohli, Nanxin Li, Jaime Rubin, Siyu Zhang, William Hobbs, Franco Locatelli

Open source

DOI
10.1182/bloodadvances.2025016702
Published
2025-12-12
Container
Blood Advances
Publisher
American Society of Hematology
Open access
unknown

Credibility signals

uncertain Score 64/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.1182/bloodadvances.2025016702,
  title = {Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel},
  author = {Josu de la Fuente and Haydar Frangoul and Peter Lang and Donna Wall and Roland Meisel and Selim Corbacioglu and Amanda M. Li and Ami J. Shah and Ben Carpenter and Janet L. Kwiatkowski and Markus Y. Mapara and Robert I. Liem and Joachim Rupprecht and Kevin H.M. Kuo and Hayley Merkeley and Mattia Algeri and Wally Smith and Puja Kohli and Nanxin Li and Jaime Rubin and Siyu Zhang and William Hobbs and Franco Locatelli},
  year = {2025},
  journal = {Blood Advances},
  doi = {10.1182/bloodadvances.2025016702},
  url = {https://doi.org/10.1182/bloodadvances.2025016702}
}

RIS

TY  - JOUR
TI  - Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel
AU  - Josu de la Fuente
AU  - Haydar Frangoul
AU  - Peter Lang
AU  - Donna Wall
AU  - Roland Meisel
AU  - Selim Corbacioglu
AU  - Amanda M. Li
AU  - Ami J. Shah
AU  - Ben Carpenter
AU  - Janet L. Kwiatkowski
AU  - Markus Y. Mapara
AU  - Robert I. Liem
AU  - Joachim Rupprecht
AU  - Kevin H.M. Kuo
AU  - Hayley Merkeley
AU  - Mattia Algeri
AU  - Wally Smith
AU  - Puja Kohli
AU  - Nanxin Li
AU  - Jaime Rubin
AU  - Siyu Zhang
AU  - William Hobbs
AU  - Franco Locatelli
PY  - 2025
JO  - Blood Advances
DO  - 10.1182/bloodadvances.2025016702
UR  - https://doi.org/10.1182/bloodadvances.2025016702
ER  - 

APA

Fuente, J. D. L., Frangoul, H., Lang, P., Wall, D., Meisel, R., Corbacioglu, S., Li, A. M., Shah, A. J., Carpenter, B., Kwiatkowski, J. L., Mapara, M. Y., Liem, R. I., Rupprecht, J., Kuo, K. H., Merkeley, H., Algeri, M., Smith, W., Kohli, P., Li, N., Rubin, J., Zhang, S., Hobbs, W., & Locatelli, F. (2025). Improvements in health-related quality of life in patients with transfusion-dependent β-thalassemia after exagamglogene autotemcel. Blood Advances. https://doi.org/10.1182/bloodadvances.2025016702

Source records