Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2.

Rasmussen CLM, Frederiksen SF, Heegaard CW, Thomsen MS, Hede E, Laczek B, Körbelin J, Wüstner D, Thomsen LB, Schwaninger M, Jensen ON, Moos T, Burkhart A

Open source

DOI
10.1186/s12987-025-00621-4
Published
2025 Jan 31
Container
Fluids and barriers of the CNS
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1186/s12987-025-00621-4,
  title = {Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2.},
  author = {Rasmussen CLM and Frederiksen SF and Heegaard CW and Thomsen MS and Hede E and Laczek B and Körbelin J and Wüstner D and Thomsen LB and Schwaninger M and Jensen ON and Moos T and Burkhart A},
  year = {2025},
  journal = {Fluids and barriers of the CNS},
  doi = {10.1186/s12987-025-00621-4},
  url = {https://doi.org/10.1186/s12987-025-00621-4}
}

RIS

TY  - JOUR
TI  - Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2.
AU  - Rasmussen CLM
AU  - Frederiksen SF
AU  - Heegaard CW
AU  - Thomsen MS
AU  - Hede E
AU  - Laczek B
AU  - Körbelin J
AU  - Wüstner D
AU  - Thomsen LB
AU  - Schwaninger M
AU  - Jensen ON
AU  - Moos T
AU  - Burkhart A
PY  - 2025
JO  - Fluids and barriers of the CNS
DO  - 10.1186/s12987-025-00621-4
UR  - https://doi.org/10.1186/s12987-025-00621-4
ER  - 

APA

CLM, R., SF, F., CW, H., MS, T., E, H., B, L., J, K., D, W., LB, T., M, S., ON, J., T, M., & A, B. (2025). Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2.. Fluids and barriers of the CNS. https://doi.org/10.1186/s12987-025-00621-4

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