Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study.

Suhr OB, Coelho T, Buades J, Pouget J, Conceicao I, Berk J, Schmidt H, Waddington-Cruz M, Campistol JM, Bettencourt BR, Vaishnaw A, Gollob J, Adams D

Open source

DOI: 10.1186/s13023-015-0326-6
Published: 2015 Sep 4
Container: Orphanet journal of rare diseases
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-015-0326-6,
  title = {Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study.},
  author = {Suhr OB and Coelho T and Buades J and Pouget J and Conceicao I and Berk J and Schmidt H and Waddington-Cruz M and Campistol JM and Bettencourt BR and Vaishnaw A and Gollob J and Adams D},
  year = {2015},
  journal = {Orphanet journal of rare diseases},
  doi = {10.1186/s13023-015-0326-6},
  url = {https://doi.org/10.1186/s13023-015-0326-6}
}

RIS

TY  - JOUR
TI  - Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study.
AU  - Suhr OB
AU  - Coelho T
AU  - Buades J
AU  - Pouget J
AU  - Conceicao I
AU  - Berk J
AU  - Schmidt H
AU  - Waddington-Cruz M
AU  - Campistol JM
AU  - Bettencourt BR
AU  - Vaishnaw A
AU  - Gollob J
AU  - Adams D
PY  - 2015
JO  - Orphanet journal of rare diseases
DO  - 10.1186/s13023-015-0326-6
UR  - https://doi.org/10.1186/s13023-015-0326-6
ER  -

APA

OB, S., T, C., J, B., J, P., I, C., J, B., H, S., M, W., JM, C., BR, B., A, V., J, G., & D, A. (2015). Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-015-0326-6

Source records

pubmed · retrieved 2026-11-10T14:42:47.060Z