Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance.

Akyol MU, Alden TD, Amartino H, Ashworth J, Belani K, Berger KI, Borgo A, Braunlin E, Eto Y, Gold JI, Jester A, Jones SA, Karsli C, Mackenzie W, Marinho DR, McFadyen A, McGill J, Mitchell JJ, Muenzer J, Okuyama T, Orchard PJ, Stevens B, Thomas S, Walker R, Wynn R, Giugliani R, Harmatz P, Hendriksz C, Scarpa M, MPS Consensus Programme Steering Committee, MPS Consensus Programme Co-Chairs

Open source

DOI: 10.1186/s13023-019-1074-9
Published: 2019 Jun 13
Container: Orphanet journal of rare diseases
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-019-1074-9,
  title = {Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance.},
  author = {Akyol MU and Alden TD and Amartino H and Ashworth J and Belani K and Berger KI and Borgo A and Braunlin E and Eto Y and Gold JI and Jester A and Jones SA and Karsli C and Mackenzie W and Marinho DR and McFadyen A and McGill J and Mitchell JJ and Muenzer J and Okuyama T and Orchard PJ and Stevens B and Thomas S and Walker R and Wynn R and Giugliani R and Harmatz P and Hendriksz C and Scarpa M and MPS Consensus Programme Steering Committee and MPS Consensus Programme Co-Chairs},
  year = {2019},
  journal = {Orphanet journal of rare diseases},
  doi = {10.1186/s13023-019-1074-9},
  url = {https://doi.org/10.1186/s13023-019-1074-9}
}

RIS

TY  - JOUR
TI  - Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance.
AU  - Akyol MU
AU  - Alden TD
AU  - Amartino H
AU  - Ashworth J
AU  - Belani K
AU  - Berger KI
AU  - Borgo A
AU  - Braunlin E
AU  - Eto Y
AU  - Gold JI
AU  - Jester A
AU  - Jones SA
AU  - Karsli C
AU  - Mackenzie W
AU  - Marinho DR
AU  - McFadyen A
AU  - McGill J
AU  - Mitchell JJ
AU  - Muenzer J
AU  - Okuyama T
AU  - Orchard PJ
AU  - Stevens B
AU  - Thomas S
AU  - Walker R
AU  - Wynn R
AU  - Giugliani R
AU  - Harmatz P
AU  - Hendriksz C
AU  - Scarpa M
AU  - MPS Consensus Programme Steering Committee
AU  - MPS Consensus Programme Co-Chairs
PY  - 2019
JO  - Orphanet journal of rare diseases
DO  - 10.1186/s13023-019-1074-9
UR  - https://doi.org/10.1186/s13023-019-1074-9
ER  -

APA

MU, A., TD, A., H, A., J, A., K, B., KI, B., A, B., E, B., Y, E., JI, G., A, J., SA, J., C, K., W, M., DR, M., A, M., J, M., JJ, M., J, M., T, O., PJ, O., B, S., S, T., R, W., R, W., R, G., P, H., C, H., M, S., Committee, M. C. P. S., & Co-Chairs, M. C. P. (2019). Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-019-1074-9

Source records

pubmed · retrieved 2026-09-25T15:04:07.499Z