Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey

Laura D’Erasmo, Antonio Gallo, Angelo Baldassare Cefalù, Alessia Di Costanzo, Samir Saheb, Antonina Giammanco, Maurizio Averna, Alessio Buonaiuto, Gabriella Iannuzzo, Giuliana Fortunato, Arturo Puja, Tiziana Montalcini, Chiara Pavanello, Laura Calabresi, Giovanni Battista Vigna, Marco Bucci, Katia Bonomo, Fabio Nota, Tiziana Sampietro, Francesco Sbrana, Patrizia Suppressa, Carlo Sabbà, Fabio Fimiani, Arturo Cesaro, Paolo Calabrò, Silvia Palmisano, Sergio D’Addato, Livia Pisciotta, Stefano Bertolini, Randa Bittar, Olga Kalmykova, Sophie Béliard, Alain Carrié, Marcello Arca, Eric Bruckert

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DOI: 10.1186/s13023-021-01999-8
Published: 2021-09-08
Container: Orphanet Journal of Rare Diseases
Publisher: Springer Science and Business Media LLC
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-021-01999-8,
  title = {Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey},
  author = {Laura D’Erasmo and Antonio Gallo and Angelo Baldassare Cefalù and Alessia Di Costanzo and Samir Saheb and Antonina Giammanco and Maurizio Averna and Alessio Buonaiuto and Gabriella Iannuzzo and Giuliana Fortunato and Arturo Puja and Tiziana Montalcini and Chiara Pavanello and Laura Calabresi and Giovanni Battista Vigna and Marco Bucci and Katia Bonomo and Fabio Nota and Tiziana Sampietro and Francesco Sbrana and Patrizia Suppressa and Carlo Sabbà and Fabio Fimiani and Arturo Cesaro and Paolo Calabrò and Silvia Palmisano and Sergio D’Addato and Livia Pisciotta and Stefano Bertolini and Randa Bittar and Olga Kalmykova and Sophie Béliard and Alain Carrié and Marcello Arca and Eric Bruckert},
  year = {2021},
  journal = {Orphanet Journal of Rare Diseases},
  doi = {10.1186/s13023-021-01999-8},
  url = {https://doi.org/10.1186/s13023-021-01999-8}
}

RIS

TY  - JOUR
TI  - Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey
AU  - Laura D’Erasmo
AU  - Antonio Gallo
AU  - Angelo Baldassare Cefalù
AU  - Alessia Di Costanzo
AU  - Samir Saheb
AU  - Antonina Giammanco
AU  - Maurizio Averna
AU  - Alessio Buonaiuto
AU  - Gabriella Iannuzzo
AU  - Giuliana Fortunato
AU  - Arturo Puja
AU  - Tiziana Montalcini
AU  - Chiara Pavanello
AU  - Laura Calabresi
AU  - Giovanni Battista Vigna
AU  - Marco Bucci
AU  - Katia Bonomo
AU  - Fabio Nota
AU  - Tiziana Sampietro
AU  - Francesco Sbrana
AU  - Patrizia Suppressa
AU  - Carlo Sabbà
AU  - Fabio Fimiani
AU  - Arturo Cesaro
AU  - Paolo Calabrò
AU  - Silvia Palmisano
AU  - Sergio D’Addato
AU  - Livia Pisciotta
AU  - Stefano Bertolini
AU  - Randa Bittar
AU  - Olga Kalmykova
AU  - Sophie Béliard
AU  - Alain Carrié
AU  - Marcello Arca
AU  - Eric Bruckert
PY  - 2021
JO  - Orphanet Journal of Rare Diseases
DO  - 10.1186/s13023-021-01999-8
UR  - https://doi.org/10.1186/s13023-021-01999-8
ER  -

APA

D’Erasmo, L., Gallo, A., Cefalù, A. B., Costanzo, A. D., Saheb, S., Giammanco, A., Averna, M., Buonaiuto, A., Iannuzzo, G., Fortunato, G., Puja, A., Montalcini, T., Pavanello, C., Calabresi, L., Vigna, G. B., Bucci, M., Bonomo, K., Nota, F., Sampietro, T., Sbrana, F., Suppressa, P., Sabbà, C., Fimiani, F., Cesaro, A., Calabrò, P., Palmisano, S., D’Addato, S., Pisciotta, L., Bertolini, S., Bittar, R., Kalmykova, O., Béliard, S., Carrié, A., Arca, M., & Bruckert, E. (2021). Long-term efficacy of lipoprotein apheresis and lomitapide in the treatment of homozygous familial hypercholesterolemia (HoFH): a cross-national retrospective survey. Orphanet Journal of Rare Diseases. https://doi.org/10.1186/s13023-021-01999-8

Source records

crossref · retrieved 2026-09-26T10:14:44.756Z