A position statement on the post gene-therapy rehabilitation of aromatic I-amino acid decarboxylase deficiency patients.

Lee HM, Mercimek-Andrews S, Horvath G, Marchese D, Poulin RE 3rd, Krolick A, Tierney KL, Turna J, Wei J, Hwu WL

Open source

DOI
10.1186/s13023-024-03019-x
Published
2024 Jan 18
Container
Orphanet journal of rare diseases
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1186/s13023-024-03019-x,
  title = {A position statement on the post gene-therapy rehabilitation of aromatic I-amino acid decarboxylase deficiency patients.},
  author = {Lee HM and Mercimek-Andrews S and Horvath G and Marchese D and Poulin RE 3rd and Krolick A and Tierney KL and Turna J and Wei J and Hwu WL},
  year = {2024},
  journal = {Orphanet journal of rare diseases},
  doi = {10.1186/s13023-024-03019-x},
  url = {https://doi.org/10.1186/s13023-024-03019-x}
}

RIS

TY  - JOUR
TI  - A position statement on the post gene-therapy rehabilitation of aromatic I-amino acid decarboxylase deficiency patients.
AU  - Lee HM
AU  - Mercimek-Andrews S
AU  - Horvath G
AU  - Marchese D
AU  - Poulin RE 3rd
AU  - Krolick A
AU  - Tierney KL
AU  - Turna J
AU  - Wei J
AU  - Hwu WL
PY  - 2024
JO  - Orphanet journal of rare diseases
DO  - 10.1186/s13023-024-03019-x
UR  - https://doi.org/10.1186/s13023-024-03019-x
ER  - 

APA

HM, L., S, M., G, H., D, M., 3rd, P. R., A, K., KL, T., J, T., J, W., & WL, H. (2024). A position statement on the post gene-therapy rehabilitation of aromatic I-amino acid decarboxylase deficiency patients.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-024-03019-x

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