Unmet needs of adults living with mucopolysaccharidosis II: data from the Hunter Outcome Survey.

Muenzer J, Amartino H, Giugliani R, Harmatz P, Lin SP, Link B, Molter D, Ramaswami U, Scarpa M, Botha J, Audi J, Burton BK

Open source

DOI: 10.1186/s13023-024-03464-8
Published: 2025 Jul 1
Container: Orphanet journal of rare diseases
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-024-03464-8,
  title = {Unmet needs of adults living with mucopolysaccharidosis II: data from the Hunter Outcome Survey.},
  author = {Muenzer J and Amartino H and Giugliani R and Harmatz P and Lin SP and Link B and Molter D and Ramaswami U and Scarpa M and Botha J and Audi J and Burton BK},
  year = {2025},
  journal = {Orphanet journal of rare diseases},
  doi = {10.1186/s13023-024-03464-8},
  url = {https://doi.org/10.1186/s13023-024-03464-8}
}

RIS

TY  - JOUR
TI  - Unmet needs of adults living with mucopolysaccharidosis II: data from the Hunter Outcome Survey.
AU  - Muenzer J
AU  - Amartino H
AU  - Giugliani R
AU  - Harmatz P
AU  - Lin SP
AU  - Link B
AU  - Molter D
AU  - Ramaswami U
AU  - Scarpa M
AU  - Botha J
AU  - Audi J
AU  - Burton BK
PY  - 2025
JO  - Orphanet journal of rare diseases
DO  - 10.1186/s13023-024-03464-8
UR  - https://doi.org/10.1186/s13023-024-03464-8
ER  -

APA

J, M., H, A., R, G., P, H., SP, L., B, L., D, M., U, R., M, S., J, B., J, A., & BK, B. (2025). Unmet needs of adults living with mucopolysaccharidosis II: data from the Hunter Outcome Survey.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-024-03464-8

Source records

pubmed · retrieved 2026-09-26T03:46:34.452Z