A phase 2 randomized, double-blind trial of ART-001, a selective PI3Kα inhibitor, for the treatment of slow-flow vascular malformations.

Ozeki M, Tanaka A, Kuniyeda K, Nozaki T, Fujino A, Nomura T, Uemura N, Suenobu S, Aramaki-Hattori N, Hayashi A, Kato A, Kiyosue H, Imagawa K, Nagao M, Shimizu F, Ochi J, Horiuchi S, Ohyama T, Ando H, Nagabukuro H

Open source

DOI: 10.1186/s13023-025-03564-z
Published: 2025 Feb 10
Container: Orphanet journal of rare diseases
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-025-03564-z,
  title = {A phase 2 randomized, double-blind trial of ART-001, a selective PI3Kα inhibitor, for the treatment of slow-flow vascular malformations.},
  author = {Ozeki M and Tanaka A and Kuniyeda K and Nozaki T and Fujino A and Nomura T and Uemura N and Suenobu S and Aramaki-Hattori N and Hayashi A and Kato A and Kiyosue H and Imagawa K and Nagao M and Shimizu F and Ochi J and Horiuchi S and Ohyama T and Ando H and Nagabukuro H},
  year = {2025},
  journal = {Orphanet journal of rare diseases},
  doi = {10.1186/s13023-025-03564-z},
  url = {https://doi.org/10.1186/s13023-025-03564-z}
}

RIS

TY  - JOUR
TI  - A phase 2 randomized, double-blind trial of ART-001, a selective PI3Kα inhibitor, for the treatment of slow-flow vascular malformations.
AU  - Ozeki M
AU  - Tanaka A
AU  - Kuniyeda K
AU  - Nozaki T
AU  - Fujino A
AU  - Nomura T
AU  - Uemura N
AU  - Suenobu S
AU  - Aramaki-Hattori N
AU  - Hayashi A
AU  - Kato A
AU  - Kiyosue H
AU  - Imagawa K
AU  - Nagao M
AU  - Shimizu F
AU  - Ochi J
AU  - Horiuchi S
AU  - Ohyama T
AU  - Ando H
AU  - Nagabukuro H
PY  - 2025
JO  - Orphanet journal of rare diseases
DO  - 10.1186/s13023-025-03564-z
UR  - https://doi.org/10.1186/s13023-025-03564-z
ER  -

APA

M, O., A, T., K, K., T, N., A, F., T, N., N, U., S, S., N, A., A, H., A, K., H, K., K, I., M, N., F, S., J, O., S, H., T, O., H, A., & H, N. (2025). A phase 2 randomized, double-blind trial of ART-001, a selective PI3Kα inhibitor, for the treatment of slow-flow vascular malformations.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-025-03564-z

Source records

pubmed · retrieved 2026-09-26T11:10:01.880Z