Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups.
- DOI
- 10.1186/s13023-026-04221-9
- Published
- 2026 Feb 5
- Container
- Orphanet journal of rare diseases
- Publisher
- Not recorded
- Open access
- yes
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limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
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Cite this work
BibTeX
@article{allodium:10.1186/s13023-026-04221-9,
title = {Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups.},
author = {de Las Heras J and Cebolla JJ and de Pedro S and Gómez-Barrera M and Vitoria I},
year = {2026},
journal = {Orphanet journal of rare diseases},
doi = {10.1186/s13023-026-04221-9},
url = {https://doi.org/10.1186/s13023-026-04221-9}
}RIS
TY - JOUR TI - Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups. AU - de Las Heras J AU - Cebolla JJ AU - de Pedro S AU - Gómez-Barrera M AU - Vitoria I PY - 2026 JO - Orphanet journal of rare diseases DO - 10.1186/s13023-026-04221-9 UR - https://doi.org/10.1186/s13023-026-04221-9 ER -
APA
J, D. L. H., JJ, C., S, D. P., M, G., & I, V. (2026). Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups.. Orphanet journal of rare diseases. https://doi.org/10.1186/s13023-026-04221-9
Source records
- pubmed · retrieved 2026-09-26T22:44:59.418Z