Should rare and ultrarare diseases be treated differently in health coverage decisions?

Livia Fernandes Probst, Renata Cristina Ferreira Rola, Viviane Karoline da Silva Carvalho, Jorge Otávio Maia Barreto, Ivan Ricardo Zimmermann, Alfredo Palacios, Ávila Teixeira Vidal, Marisa Santos, Everton Nunes da Silva

Open source

DOI
10.1186/s13023-026-04521-0
Published
2026-08-05
Container
Orphanet Journal of Rare Diseases
Publisher
Springer Science and Business Media LLC
Open access
unknown

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Cite this work

BibTeX

@article{allodium:10.1186/s13023-026-04521-0,
  title = {Should rare and ultrarare diseases be treated differently in health coverage decisions?},
  author = {Livia Fernandes Probst and Renata Cristina Ferreira Rola and Viviane Karoline da Silva Carvalho and Jorge Otávio Maia Barreto and Ivan Ricardo Zimmermann and Alfredo Palacios and Ávila Teixeira Vidal and Marisa Santos and Everton Nunes da Silva},
  year = {2026},
  journal = {Orphanet Journal of Rare Diseases},
  doi = {10.1186/s13023-026-04521-0},
  url = {https://doi.org/10.1186/s13023-026-04521-0}
}

RIS

TY  - JOUR
TI  - Should rare and ultrarare diseases be treated differently in health coverage decisions?
AU  - Livia Fernandes Probst
AU  - Renata Cristina Ferreira Rola
AU  - Viviane Karoline da Silva Carvalho
AU  - Jorge Otávio Maia Barreto
AU  - Ivan Ricardo Zimmermann
AU  - Alfredo Palacios
AU  - Ávila Teixeira Vidal
AU  - Marisa Santos
AU  - Everton Nunes da Silva
PY  - 2026
JO  - Orphanet Journal of Rare Diseases
DO  - 10.1186/s13023-026-04521-0
UR  - https://doi.org/10.1186/s13023-026-04521-0
ER  - 

APA

Probst, L. F., Rola, R. C. F., Carvalho, V. K. D. S., Barreto, J. O. M., Zimmermann, I. R., Palacios, A., Vidal, Á. T., Santos, M., & Silva, E. N. D. (2026). Should rare and ultrarare diseases be treated differently in health coverage decisions?. Orphanet Journal of Rare Diseases. https://doi.org/10.1186/s13023-026-04521-0

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