Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model

Germana Cocozza, Tiziano D’Andrea, Martina Di Rocco, Ludovica Maria Busdraghi, Gilda Chilà, Xingzi Lin, Enrico Lanza, Fanny Collaud, Francesca C. Follo, Clelia Buccheri, Viola Folli, Giuseppe Ronzitti, Ferdinando Scavizzi, Marcello Raspa, Vincenzo Leuzzi, Vladimir L. Katanaev, Serena Galosi, Sergio Fucile, Simone Martinelli, Giuseppina D’Alessandro, Cristina Limatola

Open source

DOI
10.1186/s40478-026-02389-6
Published
2026-07-21
Container
Acta Neuropathologica Communications
Publisher
Springer Science and Business Media LLC
Open access
unknown

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BibTeX

@article{allodium:10.1186/s40478-026-02389-6,
  title = {Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model},
  author = {Germana Cocozza and Tiziano D’Andrea and Martina Di Rocco and Ludovica Maria Busdraghi and Gilda Chilà and Xingzi Lin and Enrico Lanza and Fanny Collaud and Francesca C. Follo and Clelia Buccheri and Viola Folli and Giuseppe Ronzitti and Ferdinando Scavizzi and Marcello Raspa and Vincenzo Leuzzi and Vladimir L. Katanaev and Serena Galosi and Sergio Fucile and Simone Martinelli and Giuseppina D’Alessandro and Cristina Limatola},
  year = {2026},
  journal = {Acta Neuropathologica Communications},
  doi = {10.1186/s40478-026-02389-6},
  url = {https://doi.org/10.1186/s40478-026-02389-6}
}

RIS

TY  - JOUR
TI  - Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model
AU  - Germana Cocozza
AU  - Tiziano D’Andrea
AU  - Martina Di Rocco
AU  - Ludovica Maria Busdraghi
AU  - Gilda Chilà
AU  - Xingzi Lin
AU  - Enrico Lanza
AU  - Fanny Collaud
AU  - Francesca C. Follo
AU  - Clelia Buccheri
AU  - Viola Folli
AU  - Giuseppe Ronzitti
AU  - Ferdinando Scavizzi
AU  - Marcello Raspa
AU  - Vincenzo Leuzzi
AU  - Vladimir L. Katanaev
AU  - Serena Galosi
AU  - Sergio Fucile
AU  - Simone Martinelli
AU  - Giuseppina D’Alessandro
AU  - Cristina Limatola
PY  - 2026
JO  - Acta Neuropathologica Communications
DO  - 10.1186/s40478-026-02389-6
UR  - https://doi.org/10.1186/s40478-026-02389-6
ER  - 

APA

Cocozza, G., D’Andrea, T., Rocco, M. D., Busdraghi, L. M., Chilà, G., Lin, X., Lanza, E., Collaud, F., Follo, F. C., Buccheri, C., Folli, V., Ronzitti, G., Scavizzi, F., Raspa, M., Leuzzi, V., Katanaev, V. L., Galosi, S., Fucile, S., Martinelli, S., D’Alessandro, G., & Limatola, C. (2026). Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model. Acta Neuropathologica Communications. https://doi.org/10.1186/s40478-026-02389-6

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